The effectiveness and value of therapies for spinal muscular atrophy
脊髓性肌萎缩症疗法的有效性和价值
期刊:
影响因子:
doi:10.18553/jmcp.2026.32.2.230
Tice, Jeffrey A; Luu, Linda; Sanchez, Sol; Lee, Woojung; Nikitin, Dmitriy; Phillips, Marie; Carlson, Josh J; Chan, Hui-Hsuan; Rind, David M; Agboola, Foluso