Ribofuranose-based GalNAc-conjugated siRNA enhances the liver-targeted delivery and elicits robust RNAi-mediated gene silencing
基于核糖呋喃糖的 GalNAc 偶联 siRNA 可增强肝脏靶向递送,并引发强效的 RNAi 介导的基因沉默。
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102801
Huang, Ze-Ao; Li, Zhen-Min; Wang, Jie; Ji, Guang-Shen; Gao, Zhong-Cai; Chen, Ai-Fu; Tian, Zhi-Kang; Yu, Fei; Song, Geng-Shen