Neurofilament light is a treatment-responsive biomarker in CLN2 disease
神经丝轻链是CLN2疾病中一种对治疗有反应的生物标志物。
期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.50942
Ru, Yuanbin; Corado, Carley; Soon, Russell K Jr; Melton, Andrew C; Harris, Adam; Yu, Guoying K; Pryer, Nancy; Sinclair, John R; Katz, Martin L; Ajayi, Temitayo; Jacoby, David; Russell, Chris B; Chandriani, Sanjay