Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells
组合碱基编辑技术将疾病矫正与造血干细胞和祖细胞的谱系扩增相结合
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影响因子:
doi:10.64898/2026.04.13.718029
Jia, Kun; Soupene, Eric; Sinha, Roshani; Lesch, Benjamin J; Pendergast, Michael A; Choi, Rachel; Zhang, Xinyi; Foppiani, Elisabetta M; Kostamo, Zachary; Chu, Simon N; Sharma, Devesh; Yu, Xinjie; Cordero, Marco; Walters, Mark C; MacKenzie, Tippi C; Sheehan, Vivien A; Cromer, M Kyle