Allele-specific gene editing prevents deafness in a model of dominant progressive hearing loss
等位基因特异性基因编辑可预防显性进行性听力损失模型中的耳聋。
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-019-0500-9
György, Bence; Nist-Lund, Carl; Pan, Bifeng; Asai, Yukako; Karavitaki, K Domenica; Kleinstiver, Benjamin P; Garcia, Sara P; Zaborowski, Mikołaj P; Solanes, Paola; Spataro, Sofia; Schneider, Bernard L; Joung, J Keith; Géléoc, Gwenaëlle S G; Holt, Jeffrey R; Corey, David P