日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Small molecule-directed differentiation of submerged-cultured human nasal airway epithelia for respiratory disease modeling

利用小分子定向分化浸没培养的人鼻气道上皮细胞用于呼吸系统疾病建模

Dreyer, Henriette H M; Ithakisiou, Georgia-Nefeli; Spelier, Sacha; Iwanski, Malina K; Katrukha, Eugene; Terstappen, Jonne; Rodenburg, Lisa W; Shekhar, Aditi; den Hertog-Oosterhoff, Loes A; Smits, Shannon M A; van der Windt, Isabelle S; Azink, Lotte T; Bijlard, Linda H M; Passier, Koen; van Beuningen, Sam F B; Lebbink, Robert Jan; Haarman, Eric G; van der Ent, Cornelis K; Kapitein, Lukas C; Bont, Louis J; Beekman, Jeffrey M; Amatngalim, Gimano D

Patient-Derived Intestinal Organoids in the Global Cystic Fibrosis Landscape

全球囊性纤维化领域中患者来源的肠道类器官

Kroes, Suzanne; Taylor-Cousar, Jennifer L; Zampoli, Marco; Karadag, Bülent; van der Ent, Cornelis K; de Winter-de Groot, Karin M; Beekman, Jeffrey M; Spelier, Sacha

ACE-tRNAs are a platform technology for suppressing nonsense mutations that cause cystic fibrosis.

ACE-tRNA 是一种用于抑制导致囊性纤维化的无义突变的平台技术

Ko Wooree, Porter Joseph J, Spelier Sacha, Sorensen Emily G, Bhatt Priyanka, Gabell Jeffrey T, van der Windt Isabelle, Couch Tyler, Coote Kevin, Mense Martin, Beekman Jeffrey M, Lueck John D

The Promising Role of Intestinal Organoids in the Diagnostic Work-Up of Cystic Fibrosis Screen Positive Inconclusive Diagnosis/CFTR-Related Metabolic Syndrome (CFSPID/CRMS)

肠道类器官在囊性纤维化筛查阳性但诊断不确定/CFTR相关代谢综合征(CFSPID/CRMS)诊断工作中的潜在作用

Rodriguez Mier, Noelia; Destoop, Marlies; Spelier, Sacha; Ramalho, Anabela Santo; Beekman, Jeffrey M; Vermeulen, François; de Winter-de Groot, Karin M; Proesmans, Marijke

Organoid-guided synergistic treatment of minimal function CFTR mutations with CFTR modulators, roflumilast and simvastatin: a personalised approach

利用类器官引导的CFTR调节剂、罗氟司特和辛伐他汀协同治疗功能极低的CFTR突变:一种个体化方法

Spelier, Sacha; de Winter-de Groot, Karin; Keijzer-Nieuwenhuijze, Natascha; Liem, Yves; van der Ent, Kors; Beekman, Jeffrey; Kamphuis, Lieke S

CFTR Rescue in Intestinal Organoids with GLPG/ABBV-2737, ABBV/GLPG-2222 and ABBV/GLPG-2451 Triple Therapy

利用 GLPG/ABBV-2737、ABBV/GLPG-2222 和 ABBV/GLPG-2451 三联疗法在肠道类器官中挽救 CFTR 表达

de Poel, Eyleen; Spelier, Sacha; Korporaal, Ricardo; Lai, Ka Wai; Boj, Sylvia F; Conrath, Katja; van der Ent, Cornelis K; Beekman, Jeffrey M