日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of an adeno-associated virus vector for gene replacement therapy of NF1-related tumors

开发用于NF1相关肿瘤基因替代疗法的腺相关病毒载体

Ren-Yuan Bai ,Jingyi Shi ,Jianan Liu ,Nihao Sun ,Yuqing Lu ,Xiaojun Chen ,Manzhu Xu ,Hotae Lim ,Yang Li ,Huazhen Xu ,Karis Weisgerber ,Zhihong Ren ,Christine A Pratilas ,Jaishri O Blakeley ,Melissa L Fishel ,Meritxell Carrió ,Eduard Serra ,Verena Staedtke

The RXR Agonist MSU-42011 Reduces Tumor Burden in a Murine Preclinical NF1-Deficient Model.

RXR激动剂MSU-42011可降低小鼠临床前NF1缺陷模型中的肿瘤负荷

Hung Pei-Yu, Moerland Jessica A, Leal Ana S, Aleiwi Bilal, Ellsworth Edmund, Clapp D Wade, Staedtke Verena, Bai Renyuan, Liby Karen T

Pan-RAS inhibitor RMC-7977 is efficacious in treating NF1-related tumors

泛RAS抑制剂RMC-7977对治疗NF1相关肿瘤有效

Bai, Ren-Yuan; Xu, Manzhu; Lu, Yuqing; Liu, Jianan; Staedtke, Verena

Hypoxia-targeting bacteria in cancer therapy

癌症治疗中的低氧靶向细菌

Staedtke, Verena; Sun, Nihao; Bai, Renyuan

Existing and Developing Preclinical Models for Neurofibromatosis Type 1-Related Cutaneous Neurofibromas

现有和正在开发的1型神经纤维瘤病相关皮肤神经纤维瘤的临床前模型

Staedtke, Verena; Topilko, Piotr; Le, Lu Q; Grimes, Kevin; Largaespada, David A; Cagan, Ross L; Steensma, Matthew R; Stemmer-Rachamimov, Anat; Blakeley, Jaishri O; Rhodes, Steven D; Ly, Ina; Romo, Carlos G; Lee, Sang Y; Serra, Eduard

RAS Signaling Gone Awry in the Skin: The Complex Role of RAS in Cutaneous Neurofibroma Pathogenesis, Emerging Biological Insights

皮肤中RAS信号传导异常:RAS在皮肤神经纤维瘤发病机制中的复杂作用,新兴生物学见解

Rhodes, Steven D; McCormick, Frank; Cagan, Ross L; Bakker, Annette; Staedtke, Verena; Ly, Ina; Steensma, Matthew R; Lee, Sang Y; Romo, Carlos G; Blakeley, Jaishri O; Sarin, Kavita Y

Pro-905, a Novel Purine Antimetabolite, Combines with Glutamine Amidotransferase Inhibition to Suppress Growth of Malignant Peripheral Nerve Sheath Tumor

新型嘌呤抗代谢药 Pro-905 与谷氨酰胺转移酶抑制剂联合使用可抑制恶性外周神经鞘瘤的生长

Kathryn M Lemberg, Eunus S Ali, Marcela Krecmerova, Joanna Marie H Aguilar, Jesse Alt, Diane E Peters, Liang Zhao, Ying Wu, Naziba Nuha, John M Asara, Verena Staedtke, Christine A Pratilas, Pavel Majer, Rana Rais, Issam Ben-Sahra, Barbara S Slusher

Plexiform neurofibroma of the liver, with malignant transformation to MPNST, in a pediatric patient without neurofibromatosis type 1

一名未患1型神经纤维瘤病的儿童患者,其肝脏丛状神经纤维瘤发生恶性转化,发展为恶性周围神经鞘瘤(MPNST)。

Ioannou, Maria; Zhang, Lindy; Schatz, Krista; Rodriguez, Fausto J; Ahlawat, Shivani; Gocke, Christopher D; Rhee, Daniel S; Staedtke, Verena; Pratilas, Christine A

Consensus-Based Best Practice Guidelines for the Management of Spinal Deformity and Associated Tumors in Pediatric Neurofibromatosis Type 1: Screening and Surveillance, Surgical Intervention, and Medical Therapy

儿童神经纤维瘤病1型脊柱畸形及相关肿瘤管理的共识最佳实践指南:筛查和监测、手术干预和药物治疗

Xu, Amy L; Suresh, Krishna V; Gomez, Jaime A; Emans, John B; Larson, A Noelle; Cahill, Patrick J; Andras, Lindsay M; White, Klane K; Miller, Daniel J; Murphy, Joshua S; Groves, Mari L; Belzberg, Allan J; Hwang, Steven W; Rosser, Tena L; Staedtke, Verena; Ullrich, Nicole J; Sato, Aimee A; Blakeley, Jaishri O; Schorry, Elizabeth K; Gross, Andrea M; Redding, Gregory J; Sponseller, Paul D

Management of neurofibromatosis type 1-associated plexiform neurofibromas

1型神经纤维瘤病相关丛状神经纤维瘤的治疗

Fisher, Michael J; Blakeley, Jaishri O; Weiss, Brian D; Dombi, Eva; Ahlawat, Shivani; Akshintala, Srivandana; Belzberg, Allan J; Bornhorst, Miriam; Bredella, Miriam A; Cai, Wenli; Ferner, Rosalie E; Gross, Andrea M; Harris, Gordon J; Listernick, Robert; Ly, Ina; Martin, Staci; Mautner, Victor F; Salamon, Johannes M; Salerno, Kilian E; Spinner, Robert J; Staedtke, Verena; Ullrich, Nicole J; Upadhyaya, Meena; Wolters, Pamela L; Yohay, Kaleb; Widemann, Brigitte C