日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RNA editing for the treatment of alpha-1 antitrypsin deficiency.

RNA 编辑用于治疗 α-1 抗胰蛋白酶缺乏症。

Monian Prashant, Shivalila Chikdu, Lu Genliang, Bowman Keith, Briem Stearne, Bylsma Marissa, Byrne Michael, Cannon Megan, Chatterjee Arindom, Dallaire Morgan, Desai Jigar, Dufresne Jason, Faraone Alyse, Favaloro Frank, Friend Stephen, Ghosh Anamitra, Godfrey Jack, Hernandez Nidia, Huth Olivia, Iwamoto Naoki, Kawamoto Tomomi, Lamattina Anthony, Lemaitre Muriel, Lindsey Amber, Liu Fangjun, Looby Richard, Luu Khoa, McGlynn Andrew, Metterville Jake, Paik Ik-Hyeon, Pan Qianli, Patil Saurabh, Pu Tom, Purcell-Estabrook Erin, Ranade Ashwini, Rheinhardt Jeanette, Rossi Jeff, Shimizu Mamoru, Singh Kuldeep, Standley Stephany, Thomas Carina, Tripathi Snehlata, Yang Hailin, Yordanoff Ryan, Yin Yuan, Yu Hui, Narayanan PadmaKumar, Kandasamy Pachamuthu, Giangrande Paloma H, Vargeese Chandra

Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

对立体纯反义寡核苷酸进行临床前评估,以选择性降低突变型HTT的表达水平。

Iwamoto, Naoki; Liu, Yuanjing; Frank-Kamenetsky, Maria; Maguire, Abbie; Tseng, Wei Chou; Taborn, Kristin; Kothari, Nayantara; Akhtar, Ali; Bowman, Keith; Shelke, Juili Dilip; Lamattina, Anthony; Hu, Xiao Shelley; Jang, Hyun Gyung; Kandasamy, Pachamuthu; Liu, Fangjun; Longo, Ken; Looby, Richard; Meena; Metterville, Jake; Pan, Qianli; Purcell-Estabrook, Erin; Shimizu, Mamoru; Prakasha, Priyanka Shiva; Standley, Stephany; Upadhyay, Hansini; Yang, Hailin; Yin, Yuan; Zhao, Anderson; Francis, Christopher; Byrne, Mike; Dale, Elena; Verdine, Gregory L; Vargeese, Chandra

Coassembled cytotoxic and pegylated peptide amphiphiles form filamentous nanostructures with potent antitumor activity in models of breast cancer

共组装的细胞毒性肽和聚乙二醇化肽两亲分子形成丝状纳米结构,在乳腺癌模型中表现出强大的抗肿瘤活性。

Toft, Daniel J; Moyer, Tyson J; Standley, Stephany M; Ruff, Yves; Ugolkov, Andrey; Stupp, Samuel I; Cryns, Vincent L

Antitumor activity of peptide amphiphile nanofiber-encapsulated camptothecin

肽两亲分子纳米纤维包裹的喜树碱的抗肿瘤活性

Soukasene, Stephen; Toft, Daniel J; Moyer, Tyson J; Lu, Hsuming; Lee, Hyung-Kun; Standley, Stephany M; Cryns, Vincent L; Stupp, Samuel I

Induction of cancer cell death by self-assembling nanostructures incorporating a cytotoxic peptide

利用含有细胞毒性肽的自组装纳米结构诱导癌细胞死亡

Standley, Stephany M; Toft, Daniel J; Cheng, Hao; Soukasene, Stephen; Chen, Jing; Raja, Srikumar M; Band, Vimla; Band, Hamid; Cryns, Vincent L; Stupp, Samuel I