A novel dual-plasmid platform provides scalable transfection yielding improved productivity and packaging across multiple AAV serotypes and genomes
一种新型双质粒平台可实现可扩展的转染,从而提高多种AAV血清型和基因组的生产力和包装效率。
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2023.05.004
van Lieshout, Laura P; Rubin, Miranda; Costa-Grant, Katrina; Ota, Stacy; Golebiowski, Diane; Panico, Troy; Wiberg, Eli; Szymczak, Klaudia; Gilmore, Richard; Stanvick, Marissa; Burnham, Brenda; Gagnon, Jeff; Iwuchukwu, Ifeyinwa; Yang, Guang; Ghazi, Iraj; Meola, Alex; Dickerson, Ryan; Thiers, Thomas; Mustich, Luke; Hayes, April; Rivas, Israel; Lotterhand, Jason; Avila, Nancy; McGivney, James; Yin, Jin; Kelly, Tim