日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Adeno-Associated Virus Gene Transfer Ameliorates Progression of Skeletal Lesions in Mucopolysaccharidosis IVA Mice.

腺相关病毒基因转移可改善粘多糖贮积症IVA小鼠骨骼病变的进展

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2024.096
Herreño-Pachón Angélica María, Sawamoto Kazuki, Stapleton Molly, Khan Shaukat, Piechnik Matthew, Álvarez Jose Victor, Tomatsu Shunji
骨科研究
发表日期：2024
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Development of a newborn screening tool for mucopolysaccharidosis type I based on bivariate normal limits: Using glycosaminoglycan and alpha-L-iduronidase determinations on dried blood spots to predict symptoms

基于双变量正常值范围的粘多糖贮积症I型新生儿筛查工具的开发：利用干血斑中糖胺聚糖和α-L-艾杜糖醛酸酶的测定来预测症状

期刊:JIMD Reports
影响因子:1.8
doi:10.1002/jmd2.12093
Langan, Thomas J; Jalal, Kabir; Barczykowski, Amy L; Carter, Randy L; Stapleton, Molly; Orii, Kenji; Fukao, Toshiyuki; Kobayashi, Hironori; Yamaguchi, Seiji; Tomatsu, Shunji
发表日期：2020
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Safety Study of Sodium Pentosan Polysulfate for Adult Patients with Mucopolysaccharidosis Type II

戊聚糖多硫酸钠治疗成人II型粘多糖贮积症患者的安全性研究

期刊:Diagnostics
影响因子:3.3
doi:10.3390/diagnostics9040226
Orii, Kenji; Lim, Alaena; Tomatsu, Shunji; Stapleton, Molly; Suzuki, Yasuyuki; Simonaro, Calogera M; Schuchman, Edward H; Fukao, Toshiyuki; Matsumoto, Tadashi
发表日期：2019
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Hematopoietic Stem Cell Transplantation for Mucopolysaccharidoses: Past, Present, and Future

造血干细胞移植治疗粘多糖贮积症：过去、现在和未来

期刊:Biology of Blood and Marrow Transplantation
影响因子:
doi:10.1016/j.bbmt.2019.02.012
Taylor, Madeleine; Khan, Shaukat; Stapleton, Molly; Wang, Jianmin; Chen, Jing; Wynn, Robert; Yabe, Hiromasa; Chinen, Yasutsugu; Boelens, Jaap Jan; Mason, Robert W; Kubaski, Francyne; Horovitz, Dafne D G; Barth, Anneliese L; Serafini, Marta; Bernardo, Maria Ester; Kobayashi, Hironori; Orii, Kenji E; Suzuki, Yasuyuki; Orii, Tadao; Tomatsu, Shunji
细胞生物学
发育与干细胞
干细胞
发表日期：2019
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Development of Bone Targeting Drugs

骨靶向药物的研发

期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms18071345
Stapleton, Molly; Sawamoto, Kazuki; Alméciga-Díaz, Carlos J; Mackenzie, William G; Mason, Robert W; Orii, Tadao; Tomatsu, Shunji
发表日期：2017
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