Development of a novel gene editing lexicon for hemophilia: methodology and results
开发用于血友病的新型基因编辑词汇表:方法和结果
期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2025.102710
Kessler, Craig M; Valentino, Leonard A; Thornburg, Courtney D; Unzu, Carmen; Kay, Mark A; Peyvandi, Flora; Smith, Penni; Miesbach, Wolfgang; McKeown, William; Pierce, Glenn F; Khair, Kate; Starcevic, Katarina; Pillai, Monisha; Jones, Micheala; Sindhurakar, Anil; Whyte, Lauren; Delwart, Virginie; Chiao, Megan; Gutstein, David E; Antonino, Ilia; Hermans, Cedric; Pipe, Steven W