Use of pegvaliase in the management of phenylketonuria: Case series of early experience in US clinics
培伐利酶在苯丙酮尿症治疗中的应用:美国诊所早期经验病例系列
期刊:Molecular Genetics and Metabolism Reports
影响因子:1.9
doi:10.1016/j.ymgmr.2021.100790
Adams, Darius; Andersson, Hans C; Bausell, Heather; Crivelly, Kea; Eggerding, Caroline; Lah, Melissa; Lilienstein, Joshua; Lindstrom, Kristin; McNutt, Markey; Ray, Joseph W; Saavedra, Heather; Sacharow, Stephanie; Starin, Danielle; Tiffany-Amaro, Jennifer; Thomas, Janet; Vucko, Erika; Wessenberg, Leah B; Whitehall, Kaleigh