日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sustained Benefit of Blinatumomab in Infants With KMT2A-Rearranged ALL: Long-Term Outcomes, Toxicity, and Pharmacokinetics

Blinatumomab 对 KMT2A 重排 ALL 患儿的持续疗效:长期结果、毒性和药代动力学

Vieira Martins, Miguel; de Lorenzo, Paola; Kotecha, Rishi S; Attarbaschi, Andishe; Escherich, Gabriele; Nysom, Karsten; Stary, Jan; Ferster, Alina; Brethon, Benoit; Locatelli, Franco; Schrappe, Martin; Scholte-van Houtem, Peggy E; Valsecchi, Maria G; Huitema, Alwin D R; Pieters, Rob; van der Sluis, Inge M

Biological and clinical characteristics of ETV6::RUNX1-like ALL

ETV6::RUNX1样急性淋巴细胞白血病的生物学和临床特征

Zaliova, Marketa; Schinnerl, Dagmar; Boer, Judith M; Caye-Eude, Aurélie; Rehn, Jacqueline; Schwab, Claire; Arfeuille, Chloé; Attarbaschi, Andishe; Bergmann, Anke Katharina; Fiser, Karel; de Groot-Kruseman, Hester A; Haslinger, Sabrina; Inthal, Andrea; Janotova, Iveta; Lenk, Lennart; Maurer-Granofszky, Margarita; Nebral, Karin; Poyer, Fiona; Sramkova, Lucie; Stary, Jan; Strullu, Marion; Stuchly, Jan; Sutton, Rosemary; Vaskova, Martina; Winkowska, Lucie; Cario, Gunnar; Cavé, Hélène; den Boer, Monique L; Harrison, Christine; Strehl, Sabine; White, Deborah; Trka, Jan; Zuna, Jan

Comparable outcomes of HSCT up-front and after failure of IST in pediatric aplastic anemia in recent years

近年来,儿童再生障碍性贫血患者接受造血干细胞移植(HSCT)治疗,无论是否先进行免疫抑制治疗(IST),其疗效均相当。

Andresen, Felicia; Yoshimi, Ayami; Bader, Peter; Bierings, Marc; Bod'ová, Ivana; Bordon, Victoria; Buechner, Jochen; Burkhardt, Birgit; Dworzak, Michael; Erlacher, Miriam; Kállay, Krisztián; Labarque, Veerle; Locatelli, Franco; Malone, Andrea; Masmas, Tania; Müller, Ingo; Nöllke, Peter; Schmugge, Markus; Pawelec, Katarzyna; Sedlacek, Petr; Sevilla, Julian; Smith, Owen; Stary, Jan; Niemeyer, Charlotte; Strahm, Brigitte

NGS-MRD negativity in post-HSCT ALL spares unnecessary therapeutic interventions triggered by borderline qPCR results without an increase in relapse risk

在造血干细胞移植后急性淋巴细胞白血病(ALL)患者中,NGS-MRD阴性可避免因qPCR结果临界值而引发的不必要治疗干预,且不会增加复发风险。

Seferna, Krystof; Svaton, Michael; Rennerova, Andrea; Skotnicova, Aneta; Reznickova, Leona; Valova, Tatana; Sedlacek, Petr; Riha, Petr; Formankova, Renata; Keslova, Petra; Sramkova, Lucie; Stary, Jan; Zuna, Jan; Kolenova, Alexandra; Salek, Cyril; Trka, Jan; Fronkova, Eva

Results in pediatric T-ALL patients treated in trial AIEOP-BFM ALL 2009: Prognostic factors in the context of modern risk-adapted therapy

AIEOP-BFM ALL 2009 试验中接受治疗的儿童 T 细胞急性淋巴细胞白血病 (T-ALL) 患者的结果:现代风险适应性治疗背景下的预后因素

Cario, Gunnar; Valsecchi, Maria Grazia; Conter, Valentino; Gotti, Giacomo; Möricke, Anja; Stanulla, Martin; Vossen-Gajcy, Michaela; Lenk, Lennart; Stary, Jan; Hrusak, Ondrej; Dworzak, Michael; Attarbaschi, Andishe; Barbaric, Draga; Locatelli, Franco; Bodmer, Nicole; Elitzur, Sarah; Silvestri, Daniela; Dalla-Pozza, Luciano; Fagioli, Franca; Kulozik, Andreas E; Izraeli, Shai; Rizzari, Carmelo; Rademacher, Annika; Buldini, Barbara; Bourquin, Jean-Pierre; Zimmermann, Martin; Schrappe, Martin; Biondi, Andrea

Distinct pattern of genomic breakpoints in CML and BCR::ABL1-positive ALL: analysis of 971 patients

慢性粒细胞白血病和 BCR::ABL1 阳性急性淋巴细胞白血病基因组断点的独特模式:971 例患者的分析

Hovorkova, Lenka; Winkowska, Lucie; Skorepova, Justina; Krumbholz, Manuela; Benesova, Adela; Polivkova, Vaclava; Alten, Julia; Bardini, Michela; Meyer, Claus; Kim, Rathana; Trahair, Toby N; Clappier, Emmanuelle; Chiaretti, Sabina; Henderson, Michelle; Sutton, Rosemary; Sramkova, Lucie; Stary, Jan; Polakova, Katerina Machova; Marschalek, Rolf; Metzler, Markus; Cazzaniga, Giovanni; Cario, Gunnar; Trka, Jan; Zaliova, Marketa; Zuna, Jan

Biologic and Clinical Analysis of Childhood Gamma Delta T-ALL Identifies LMO2/STAG2 Rearrangements as Extremely High Risk.

儿童 Gamma Delta T-ALL 的生物学和临床分析表明 LMO2/STAG2 重排具有极高风险

Kimura Shunsuke, Park Chun Shik, Montefiori Lindsey E, Iacobucci Ilaria, Pölönen Petri, Gao Qingsong, Arnold Elizabeth D, Attarbaschi Andishe, Brown Anthony, Buldini Barbara, Caldwell Kenneth J, Chang Yunchao, Chen Chelsey, Cheng Cheng, Cheng Zhongshan, Choi John, Conter Valentino, Crews Kristine R, de Groot-Kruseman Hester A, Deguchi Takao, Eguchi Mariko, Muhle Hannah E, Elitzur Sarah, Escherich Gabriele, Freeman Burgess B 3rd, Gu Zhaohui, Han Katie, Horibe Keizo, Imamura Toshihiko, Jeha Sima, Kato Motohiro, Chiew Kean H, Khan Tanya, Kicinski Michal, Köhrer Stefan, Kornblau Steven M, Kotecha Rishi S, Li Chi-Kong, Liu Yen-Chun, Locatelli Franco, Luger Selina M, Paietta Elisabeth M, Manabe Atsushi, Marquart Hanne V, Masetti Riccardo, Maybury Mellissa, Mazilier Pauline, Meijerink Jules P P, Mitchell Sharnise, Miyamura Takako, Moore Andrew S, Oshima Koichi, Pawinska-Wasikowska Katarzyna, Pieters Rob, Prater Mollie S, Pruett-Miller Shondra M, Pui Ching-Hon, Qu Chunxu, Reiterova Michaela, Reyes Noemi, Roberts Kathryn G, Rowe Jacob M, Sato Atsushi, Schmiegelow Kjeld, Schrappe Martin, Shen Shuhong, Skoczeń Szymon, Spinelli Orietta, Stary Jan, Svaton Michael, Takagi Masatoshi, Takita Junko, Tang Yanjing, Teachey David T, Thomas Paul G, Tomizawa Daisuke, Trka Jan, Varotto Elena, Vincent Tiffaney L, Yang Jun J, Yeoh Allen E J, Zhou Yinmei, Zimmermann Martin, Inaba Hiroto, Mullighan Charles G

Genomic DNA-based measurable residual disease monitoring in pediatric acute myeloid leukemia: unselected consecutive cohort study

基于基因组DNA的儿童急性髓系白血病可测量残留病灶监测:一项非选择性连续队列研究

Zaliova, Marketa; Zuna, Jan; Winkowska, Lucie; Janotova, Iveta; Skorepova, Justina; Lukes, Julius; Meyer, Claus; Marschalek, Rolf; Novak, Zbynek; Domansky, Jiri; Stary, Jan; Sramkova, Lucie; Trka, Jan

Spontaneous remission and loss of monosomy 7: a window of opportunity for young children with SAMD9L syndrome

自发缓解和7号染色体单体消失:SAMD9L综合征患儿的治疗良机

Erlacher, Miriam; Andresen, Felicia; Sukova, Martina; Stary, Jan; De Moerloose, Barbara; Bosch, Jutte van der Werff Ten; Dworzak, Michael; Seidel, Markus G; Polychronopoulou, Sophia; Beier, Rita; Kratz, Christian P; Nathrath, Michaela; Frühwald, Michael C; Göhring, Gudrun; Bergmann, Anke K; Mayerhofer, Christina; Lebrecht, Dirk; Ramamoorthy, Senthilkumar; Yoshimi, Ayami; Strahm, Brigitte; Wlodarski, Marcin W; Niemeyer, Charlotte M

No clear benefit of preventive cranial radiotherapy in childhood Philadelphia-positive acute lymphoblastic leukemia: a retrospective analysis of the EsPhALL2010 study

儿童费城染色体阳性急性淋巴细胞白血病预防性颅脑放疗并无明显益处:EsPhALL2010 研究的回顾性分析

Conter, Valentino; Valsecchi, Maria Grazia; De Lorenzo, Paola; Gandemer, Virginie; Heyman, Mats; Saha, Vaskar; Diaz, Paulina; Li, Chi-Kong; Attarbaschi, Andishe; Escherich, Gabriele; Stary, Jan; Schrappe, Martin; Pieters, Rob; Cario, Gunnar; Biondi, Andrea