Gene Therapy for Spinal Muscular Atrophy (SMA): A Review of Current Challenges and Safety Considerations for Onasemnogene Abeparvovec (Zolgensma)
脊髓性肌萎缩症 (SMA) 的基因治疗：Onasemnogene Abeparvovec (Zolgensma) 当前挑战和安全性考虑的综述
期刊:Cureus Journal of Medical Science
影响因子:1.3
doi:10.7759/cureus.36197
Ogbonmide, Tolu; Rathore, Rajni; Rangrej, Shahid B; Hutchinson, Stedrea; Lewis, Marcia; Ojilere, Stephenie; Carvalho, Victoria; Kelly, Irenaissia
