Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides
利用新型ZEN修饰寡核苷酸,将体外剪接转换活性与体内系统递送相关联
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1038/mtna.2014.63
Hammond, Suzan M; McClorey, Graham; Nordin, Joel Z; Godfrey, Caroline; Stenler, Sofia; Lennox, Kim A; Smith, C I Edvard; Jacobi, Ashley M; Varela, Miguel A; Lee, Yi; Behlke, Mark A; Wood, Matthew J A; Andaloussi, Samir E L