日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Standardized Preclinical In Vitro Blood-Brain Barrier Mouse Assay Validates Endocytosis-Dependent Antibody Transcytosis Using Transferrin-Receptor-Mediated Pathways.

标准化的临床前体外血脑屏障小鼠试验验证了利用转铁蛋白受体介导途径的内吞依赖性抗体转胞吞作用

Morrison Jamie I, Petrovic Alex, Metzendorf Nicole G, Rofo Fadi, Yilmaz Canan U, Stenler Sofia, Laudon Hanna, Hultqvist Greta

Non-uniform dystrophin re-expression after CRISPR-mediated exon excision in the dystrophin/utrophin double-knockout mouse model of DMD

在DMD的肌营养不良蛋白/肌营养蛋白双敲除小鼠模型中,CRISPR介导的外显子切除后肌营养不良蛋白的重新表达不均匀。

Hanson, Britt; Stenler, Sofia; Ahlskog, Nina; Chwalenia, Katarzyna; Svrzikapa, Nenad; Coenen-Stass, Anna M L; Weinberg, Marc S; Wood, Matthew J A; Roberts, Thomas C

Micro-minicircle Gene Therapy: Implications of Size on Fermentation, Complexation, Shearing Resistance, and Expression

微型环状基因疗法:尺寸对发酵、络合、抗剪切性和表达的影响

Stenler, Sofia; Wiklander, Oscar Pb; Badal-Tejedor, Maria; Turunen, Janne; Nordin, Joel Z; Hallengärd, David; Wahren, Britta; Andaloussi, Samir El; Rutland, Mark W; Smith, C I Edvard; Lundin, Karin E; Blomberg, Pontus

Correlating In Vitro Splice Switching Activity With Systemic In Vivo Delivery Using Novel ZEN-modified Oligonucleotides

利用新型ZEN修饰寡核苷酸,将体外剪接转换活性与体内系统递送相关联

Hammond, Suzan M; McClorey, Graham; Nordin, Joel Z; Godfrey, Caroline; Stenler, Sofia; Lennox, Kim A; Smith, C I Edvard; Jacobi, Ashley M; Varela, Miguel A; Lee, Yi; Behlke, Mark A; Wood, Matthew J A; Andaloussi, Samir E L

Safety and efficacy of DNA vaccines: plasmids vs. minicircles

DNA疫苗的安全性和有效性:质粒与微环

Stenler, Sofia; Blomberg, Pontus; Smith, C I Edvard