日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Natural History of Children and Adolescents With Dravet Syndrome: A 24-Month Follow-Up

Dravet综合征患儿及青少年自然病程:24个月随访

Sullivan, Joseph; Wirrell, Elaine C; Knupp, Kelly G; Ciliberto, Michael; Ziobro, Julie; Chen, Dillon Y; Flamini, J Robert; Zafar, Muhammad; LaVallee, Nicole; Stepanians, Miganush; Ventola, Pam; Chavan, Tanmay S; Wang, Fei; Parkerson, Kimberly A; Ticho, Barry

Neuropsychological endpoints for clinical trials in methylmalonic acidemia and propionic acidemia: A pilot study

甲基丙二酸血症和丙酸血症临床试验的神经心理学终点:一项初步研究

Chapman, Kimberly A; MacEachern, Devon; Cox, Gerald F; Waller, Mavis; Fogarty, Jeanine; Granger, Suzanne; Stepanians, Miganush; Waisbren, Susan

DUET: A Phase 2 Study Evaluating the Efficacy and Safety of Sparsentan in Patients with FSGS

DUET:一项评估 Sparsentan 治疗 FSGS 患者疗效和安全性的 II 期研究

Trachtman, Howard; Nelson, Peter; Adler, Sharon; Campbell, Kirk N; Chaudhuri, Abanti; Derebail, Vimal Kumar; Gambaro, Giovanni; Gesualdo, Loreto; Gipson, Debbie S; Hogan, Jonathan; Lieberman, Kenneth; Marder, Brad; Meyers, Kevin Edward; Mustafa, Esmat; Radhakrishnan, Jai; Srivastava, Tarak; Stepanians, Miganush; Tesar, Vladimír; Zhdanova, Olga; Komers, Radko

Predictors of Treatment Response to Tesamorelin, a Growth Hormone-Releasing Factor Analog, in HIV-Infected Patients with Excess Abdominal Fat

预测HIV感染合并腹部脂肪过多患者对生长激素释放因子类似物替沙莫林治疗反应的因素

Mangili, Alexandra; Falutz, Julian; Mamputu, Jean-Claude; Stepanians, Miganush; Hayward, Brooke