Correction of human phospholamban R14del mutation associated with cardiomyopathy using targeted nucleases and combination therapy
使用靶向核酸酶和联合疗法纠正与心肌病相关的人类受磷蛋白 R14del 突变
期刊:Nature Communications
影响因子:14.7
doi:10.1038/ncomms7955
Ioannis Karakikes, Francesca Stillitano, Mathieu Nonnenmacher, Christos Tzimas, Despina Sanoudou, Vittavat Termglinchan, Chi-Wing Kong, Stephanie Rushing, Jens Hansen, Delaine Ceholski, Fotis Kolokathis, Dimitrios Kremastinos, Alexandros Katoulis, Lihuan Ren, Ninette Cohen, Johannes M I H Gho, Dimit