日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Correction of human phospholamban R14del mutation associated with cardiomyopathy using targeted nucleases and combination therapy

使用靶向核酸酶和联合疗法纠正与心肌病相关的人类受磷蛋白 R14del 突变

Ioannis Karakikes, Francesca Stillitano, Mathieu Nonnenmacher, Christos Tzimas, Despina Sanoudou, Vittavat Termglinchan, Chi-Wing Kong, Stephanie Rushing, Jens Hansen, Delaine Ceholski, Fotis Kolokathis, Dimitrios Kremastinos, Alexandros Katoulis, Lihuan Ren, Ninette Cohen, Johannes M I H Gho, Dimit