日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Interleukin-15-armoured GPC3 CAR T cells for patients with solid cancers

用于治疗实体瘤患者的白细胞介素-15修饰的GPC3 CAR T细胞

David Steffin ,Nisha Ghatwai ,Antonino Montalbano ,Purva Rathi ,Amy N Courtney ,Azlann B Arnett ,Julien Fleurence ,Ramy Sweidan ,Tao Wang ,Huimin Zhang ,Prakash Masand ,John M Maris ,Daniel Martinez ,Jennifer Pogoriler ,Navin Varadarajan ,Sachin G Thakkar ,Deborah Lyon ,Natalia Lapteva ,Mei Zhuyong ,Kalyani Patel ,Dolores Lopez-Terrada ,Carlos A Ramos ,Premal Lulla ,Tannaz Armaghany ,Bambi J Grilley ,Stephen Gottschalk ,Gianpietro Dotti ,Leonid S Metelitsa ,Helen E Heslop ,Malcolm K Brenner ,Pavel Sumazin ,Andras Heczey

VDAC2 loss elicits tumour destruction and inflammation for cancer therapy

VDAC2缺失可引发肿瘤破坏和炎症,从而促进癌症治疗。

Sujing Yuan # ,Renqiang Sun # ,Hao Shi ,Nicole M Chapman ,Haoran Hu ,Cliff Guy ,Sherri Rankin ,Anil Kc ,Gustavo Palacios ,Xiaoxi Meng ,Xiang Sun ,Peipei Zhou ,Xiaoyang Yang ,Stephen Gottschalk ,Hongbo Chi

Innate-like memory T cells rapidly emerge in humans after gene therapy for SCID-X1

SCID-X1基因治疗后,人体内会迅速出现先天样记忆T细胞。

Anoop Babu Vasandan ,Hossam A Abdelsamed ,Shannon K Boi ,Grace Ward ,Shanta Alli ,Tian Mi ,Xin Lan ,Xusheng Zhang ,Morton J Cowan ,Jennifer M Puck ,Aleksandra Petrovic ,David Rawlings ,Albert Zhou ,Ewelina Mamcarz ,Stephen Gottschalk ,Caitlin C Zebley ,Ben Youngblood

Preclinical development of lentiviral vector gene therapy for Diamond-Blackfan anemia syndrome

针对Diamond-Blackfan贫血综合征的慢病毒载体基因疗法的临床前开发

Senthil Velan Bhoopalan,Thiyagaraj Mayuranathan,Nana Liu,Kalin Mayberry,Yu Yao,Jingjing Zhang,Jean-Yves Métais,Koon-Kiu Yan,Robert E Throm,Steven R Ellis,Yan Ju,Lei Han,Shruthi Suryaprakash,Lance E Palmer,Sheng Zhou,Jiyang Yu,Yong Cheng,Jonathan S Yen,Stephen Gottschalk,Mitchell J Weiss

Discovery of immunotherapy targets for pediatric solid and brain tumors by exon-level expression

通过外显子水平表达发现儿童实体瘤和脑肿瘤的免疫治疗靶点

Timothy I Shaw #,Jessica Wagner #,Liqing Tian #,Elizabeth Wickman,Suresh Poudel,Jian Wang,Robin Paul,Selene C Koo,Meifen Lu,Heather Sheppard,Yiping Fan,Francis H O'Neill,Ching C Lau,Xin Zhou,Jinghui Zhang,Stephen Gottschalk

Secondary bone marrow graft loss after third-party virus-specific T cell infusion: Case report of a rare complication

第三方病毒特异性T细胞输注后继发性骨髓移植失败:罕见并发症病例报告

Michael D Keller #,Stefan A Schattgen #,Shanmuganathan Chandrakasan,E Kaitlynn Allen,Mariah A Jensen-Wachspress,Christopher A Lazarski,Muna Qayed,Haili Lang,Patrick J Hanley,Jay Tanna,Sung-Yun Pai,Suhag Parikh,Seth I Berger,Stephen Gottschalk,Michael A Pulsipher,Paul G Thomas,Catherine M Bollard

DNAJB1-PRKACA fusion neoantigens elicit rare endogenous T cell responses that potentiate cell therapy for fibrolamellar carcinoma

DNAJB1-PRKACA融合新抗原可诱导罕见的内源性T细胞反应,从而增强纤维板层癌的细胞疗法疗效。

Allison M Kirk ,Jeremy Chase Crawford ,Ching-Heng Chou ,Cliff Guy ,Kirti Pandey ,Tanya Kozlik ,Ravi K Shah ,Shanzou Chung ,Phuong Nguyen ,Xiaoyu Zhang ,Jin Wang ,Matthew Bell ,Robert C Mettelman ,E Kaitlynn Allen ,Mikhail V Pogorelyy ,Hyunjin Kim ,Anastasia A Minervina ,Walid Awad ,Resha Bajracharya ,Toni White ,Donald Long Jr ,Brittney Gordon ,Michelle Morrison ,Evan S Glazer ,Andrew J Murphy ,Yixing Jiang ,Elizabeth A Fitzpatrick ,Mark Yarchoan ,Praveen Sethupathy ,Nathan P Croft ,Anthony W Purcell ,Sara M Federico ,Elizabeth Stewart ,Stephen Gottschalk ,Anthony E Zamora ,Christopher DeRenzo ,Scott E Strome ,Paul G Thomas

Peptide-scFv antigen recognition domains effectively confer CAR T cell multiantigen specificity

肽-scFv抗原识别域有效赋予CAR T细胞多抗原特异性

Jaquelyn T Zoine,Kalyan Immadisetty,Jorge Ibanez-Vega,Sarah E Moore,Chris Nevitt,Unmesha Thanekar,Liqing Tian,Abbas Karouni,Peter J Chockley,Bright Arthur,Heather Sheppard,Jeffery M Klco,Deanna M Langfitt,Giedre Krenciute,Stephen Gottschalk,M Madan Babu,M Paulina Velasquez

DNAJB1-PRKACA fusion neoantigens elicit rare endogenous T cell responses that potentiate cell therapy for fibrolamellar carcinoma

DNAJB1-PRKACA融合新抗原可诱导罕见的内源性T细胞反应,从而增强纤维板层癌的细胞疗法疗效。

Allison M Kirk,Jeremy Chase Crawford,Ching-Heng Chou,Cliff Guy,Kirti Pandey,Tanya Kozlik,Ravi K Shah,Shanzou Chung,Phuong Nguyen,Xiaoyu Zhang,Jin Wang,Matthew Bell,Robert C Mettelman,E Kaitlynn Allen,Mikhail V Pogorelyy,Hyunjin Kim,Anastasia A Minervina,Walid Awad,Resha Bajracharya,Toni White,Donald Long Jr,Brittney Gordon,Michelle Morrison,Evan S Glazer,Andrew J Murphy,Yixing Jiang,Elizabeth A Fitzpatrick,Mark Yarchoan,Praveen Sethupathy,Nathan P Croft,Anthony W Purcell,Sara M Federico,Elizabeth Stewart,Stephen Gottschalk,Anthony E Zamora,Christopher DeRenzo,Scott E Strome,Paul G Thomas

IL-18R supported CAR T cells targeting oncofetal tenascin C for the immunotherapy of pediatric sarcoma and brain tumors

IL-18R支持的CAR T细胞靶向癌胚腱蛋白C,用于儿童肉瘤和脑肿瘤的免疫治疗

Elizabeth Wickman ,Shannon Lange ,Jessica Wagner ,Jorge Ibanez ,Liqing Tian ,Meifen Lu ,Heather Sheppard ,Jason Chiang ,Selene C Koo ,Peter Vogel ,Deanna Langfitt ,S Scott Perry ,Raghuvaran Shanmugam ,Matthew Bell ,Timothy I Shaw ,Giedre Krenciute ,Jinghui Zhang ,Stephen Gottschalk