Dual mRNA therapy restores metabolic function in long-term studies in mice with propionic acidemia
双重 mRNA 疗法在患有丙酸血症的小鼠的长期研究中恢复了代谢功能
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-020-19156-3
Lei Jiang, Ji-Sun Park, Ling Yin, Rodrigo Laureano, Eric Jacquinet, Jinsong Yang, Shi Liang, Andrea Frassetto, Jenny Zhuo, Xinhua Yan, Xuling Zhu, Steven Fortucci, Kara Hoar, Cosmin Mihai, Christopher Tunkey, Vlad Presnyak, Kerry E Benenato, Christine M Lukacs, Paolo G V Martini, Lin T Guey