Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo
γ 逆转录病毒介导的 SCID-X1 纠正与体内载体整合位点分布不均有关
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI31661
Kerstin Schwarzwaelder, Steven J Howe, Manfred Schmidt, Martijn H Brugman, Annette Deichmann, Hanno Glimm, Sonja Schmidt, Claudia Prinz, Manuela Wissler, Douglas J S King, Fang Zhang, Kathryn L Parsley, Kimberly C Gilmour, Joanna Sinclair, Jinhua Bayford, Rachel Peraj, Karin Pike-Overzet, Frank J T