Recommendations for the management of MPS VI: systematic evidence- and consensus-based guidance
MPS VI 管理建议:基于系统证据和共识的指导
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-019-1080-y
Akyol, Mehmet Umut; Alden, Tord D; Amartino, Hernan; Ashworth, Jane; Belani, Kumar; Berger, Kenneth I; Borgo, Andrea; Braunlin, Elizabeth; Eto, Yoshikatsu; Gold, Jeffrey I; Jester, Andrea; Jones, Simon A; Karsli, Cengiz; Mackenzie, William; Marinho, Diane Ruschel; McFadyen, Andrew; McGill, Jim; Mitchell, John J; Muenzer, Joseph; Okuyama, Torayuki; Orchard, Paul J; Stevens, Bob; Thomas, Sophie; Walker, Robert; Wynn, Robert; Giugliani, Roberto; Harmatz, Paul; Hendriksz, Christian; Scarpa, Maurizio