日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Identifying multiscale translational safety biomarkers using a network-based systems approach

使用基于网络的系统方法识别多尺度转化安全性生物标志物

Giulia Callegaro, Johannes P Schimming, Janet Piñero González, Steven J Kunnen, Lukas Wijaya, Panuwat Trairatphisan, Linda van den Berk, Kim Beetsma, Laura I Furlong, Jeffrey J Sutherland, Jennifer Mollon, James L Stevens, Bob van de Water

Addressing the need for patient-friendly medical communications: adaptation of the 2019 recommendations for the management of MPS VI and MPS IVA

满足患者对易于理解的医疗沟通的需求:对2019年MPS VI和MPS IVA管理建议的调整

Bruce, Iain A; Ezgü, Fatih S; Kampmann, Christoph; Kenis, Vladimir; Mackenzie, William; Stevens, Bob; Walker, Robert; Hendriksz, Christian

Elosulfase alfa in the treatment of mucopolysaccharidosis type IVA: insights from the first managed access agreement

埃洛硫酸酶α治疗IVA型粘多糖贮积症:首个管理准入协议的启示

Stevens, Bob; Kenny, Tom; Thomas, Sophie; Morrison, Alexandra; Jarrett, James; Jain, Mohit

A co-culture nanofibre scaffold model of neural cell degeneration in relevance to Parkinson's disease.

帕金森病相关神经细胞退化的共培养纳米纤维支架模型

Chemmarappally Joseph M, Pegram Henry C N, Abeywickrama Neranga, Fornari Enzo, Hargreaves Alan J, De Girolamo Luigi A, Stevens Bob

Recommendations for the management of MPS VI: systematic evidence- and consensus-based guidance

MPS VI 管理建议:基于系统证据和共识的指导

Akyol, Mehmet Umut; Alden, Tord D; Amartino, Hernan; Ashworth, Jane; Belani, Kumar; Berger, Kenneth I; Borgo, Andrea; Braunlin, Elizabeth; Eto, Yoshikatsu; Gold, Jeffrey I; Jester, Andrea; Jones, Simon A; Karsli, Cengiz; Mackenzie, William; Marinho, Diane Ruschel; McFadyen, Andrew; McGill, Jim; Mitchell, John J; Muenzer, Joseph; Okuyama, Torayuki; Orchard, Paul J; Stevens, Bob; Thomas, Sophie; Walker, Robert; Wynn, Robert; Giugliani, Roberto; Harmatz, Paul; Hendriksz, Christian; Scarpa, Maurizio

Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance

MPS IVA 管理建议:基于系统证据和共识的指导

Akyol, Mehmet Umut; Alden, Tord D; Amartino, Hernan; Ashworth, Jane; Belani, Kumar; Berger, Kenneth I; Borgo, Andrea; Braunlin, Elizabeth; Eto, Yoshikatsu; Gold, Jeffrey I; Jester, Andrea; Jones, Simon A; Karsli, Cengiz; Mackenzie, William; Marinho, Diane Ruschel; McFadyen, Andrew; McGill, Jim; Mitchell, John J; Muenzer, Joseph; Okuyama, Torayuki; Orchard, Paul J; Stevens, Bob; Thomas, Sophie; Walker, Robert; Wynn, Robert; Giugliani, Roberto; Harmatz, Paul; Hendriksz, Christian; Scarpa, Maurizio

Microcrystal manipulation with laser tweezers

利用激光镊子操控微晶

Wagner, Armin; Duman, Ramona; Stevens, Bob; Ward, Andy