A phase 3 randomized trial of mavorixafor, a CXCR4 antagonist, for WHIM syndrome
一项针对WHIM综合征的3期随机试验,评估CXCR4拮抗剂mavorixafor的疗效。
期刊:Blood
影响因子:23.1
doi:10.1182/blood.2023022658
Badolato, Raffaele; Alsina, Laia; Azar, Antoine; Bertrand, Yves; Bolyard, Audrey A; Dale, David; Deyà-Martínez, Àngela; Dickerson, Kathryn E; Ezra, Navid; Hasle, Henrik; Kang, Hyoung Jin; Kiani-Alikhan, Sorena; Kuijpers, Taco W; Kulagin, Alexander; Langguth, Daman; Levin, Carina; Neth, Olaf; Olbrich, Peter; Peake, Jane; Rodina, Yulia; Rutten, Caroline E; Shcherbina, Anna; Tarrant, Teresa K; Vossen, Matthias G; Wysocki, Christian A; Belschner, Andrea; Bridger, Gary J; Chen, Kelly; Dubuc, Susan; Hu, Yanping; Jiang, Honghua; Li, Sunny; MacLeod, Rick; Stewart, Murray; Taveras, Arthur G; Yan, Tina; Donadieu, Jean