日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Multiselective RAS(ON) inhibition targets oncogenic RAS and overcomes RAS-mediated resistance to FLT3i and BCL2i in AML

多选择性 RAS(ON) 抑制剂靶向致癌 RAS,并克服急性髓系白血病 (AML) 中 RAS 介导的对 FLT3 抑制剂和 BCL2 抑制剂的耐药性。

Popescu, Bogdan; Jones, Matthew F; Piao, Madison; Tran, Elaine; Koh, Andrew; Lomeli, Isabelle; Peretz, Cheryl A C; Murad, Natalia; Abelson, Sydney; Morales, Carolina; Rivera, Jose M; Batingana, Alexa Rane; D'Souza, Jeevitha; Pikman, Yana; Cheng, Michael L; Logan, Aaron C; Huang, Benjamin J; Stieglitz, Elliot; Smith, Catherine C

Therapy by omission: observation as a strategy in JMML

放任疗法:观察作为幼年型多发性骨髓瘤的治疗策略

Stieglitz, Elliot

Targeting high-risk multiple myeloma genotypes with optimized anti-CD70 CAR T cells

利用优化的抗CD70 CAR-T细胞靶向高危多发性骨髓瘤基因型

Kasap, Corynn; Izgutdina, Adila; Patiño-Escobar, Bonell; Kang, Amrik S; Chilakapati, Nikhil; Akagi, Naomi; Manoj, Ananya; Johnson, Haley; Rashid, Tasfia; Werner, Juwita; Barpanda, Abhilash; Geng, Huimin; Lin, Yu-Hsiu T; Rampersaud, Sham; Gil-Alós, Daniel; Sobh, Amin; Dupéré-Richer, Daphné; Aleman, Adolfo; Wicaksono, Gianina; Kelii, K M Kawehi; Dalal, Radhika; Ramos, Emilio; Vijayanarayanan, Anjanaa; Lakhani, Kiran; Salangsang, Fernando; Phojanakong, Paul; Camara Serrano, Juan Antonio; Zakraoui, Ons; Tariq, Isa; Chari, Ajai; Chung, Alfred; Kumar, Anupama D; Martin, Thomas G 3rd; Wolf, Jeffrey; Wong, Sandy W; Steri, Veronica; Shanmugam, Mala; Boise, Lawrence H; Kortemme, Tanja; Parekh, Samir; Stieglitz, Elliot; Licht, Jonathan D; Karlon, William J; Barwick, Benjamin G; Wiita, Arun P

Biallelic SH2B3 germline variants are associated with a neonatal myeloproliferative disease and multisystemic involvement

SH2B3基因双等位基因变异与新生儿骨髓增生性疾病和多系统受累相关。

Leardini, Davide; Flex, Elisabetta; Stieglitz, Elliot; Cerasi, Sara; Bertuccio, Salvatore Nicola; Baccelli, Francesco; Kállay, Krisztián; Kjollerstrom, Paula; Batalha, Sara; Carpentieri, Giovanna; Pedace, Lucia; Ciolfi, Andrea; Hammad, Mahmoud; Miranda, Maria; Rojas, Marta; Rao, Anupama; Innes, Andrew J; Rudelius, Martina; Santini, Valeria; Raddi, Marco; Teh, Kok-Hoi; De Vito, Rita; Yoshimi, Ayami; Tartaglia, Marco; Locatelli, Franco; Niemeyer, Charlotte M; Masetti, Riccardo

Azacytidine Monotherapy in an Infant With Mosaic NRAS-Driven Juvenile Myelomonocytic Leukemia

阿扎胞苷单药治疗嵌合型NRAS驱动的幼年型骨髓单核细胞白血病患儿

Grenier, Jeremy M; Tasian, Sarah K; Stieglitz, Elliot; Abdullaev, Zied; Wertheim, Gerald B; Li, Marilyn M; Phillips, Charles A

Thrombopoietin Receptor Agonists for Thrombocytopenia in Pediatric Hematologic Malignancies

血小板生成素受体激动剂治疗儿童血液系统恶性肿瘤引起的血小板减少症

Marinoff, Amanda E; Thrall, Allyson; Aaronson, Kathryn; Braun, Benjamin S; Castellanos, Maria; Chu, Julia; Hermiston, Michelle; Huang, Benjamin J; Levinson, Anya; Southworth, Erica; Winger, Beth Apsel; Olshen, Adam; Stieglitz, Elliot

Juvenile myelomonocytic leukemia stem cells are sensitive to NK cell-mediated lysis and express targetable antigens

幼年型骨髓单核细胞白血病干细胞对NK细胞介导的溶解作用敏感,并表达可靶向的抗原。

Martinez, Shannalee; Senyukov, Vladimir V; Hasgur, Suheyla; Aquino-López, Arianexys; Emanuel, Peter D; Liu, Y Lucy; Stieglitz, Elliot; Behbehani, Gregory; Campbell, Amanda R; Lee, Dean A

Genomic landscape and clonal architecture in pediatric myeloid neoplasms with chromosome 7 deletions

染色体 7 缺失的儿童髓系肿瘤的基因组图谱和克隆结构

Westover, Tamara; Walsh, Michael P; Abdelhamed, Sherif; Xiong, Emily; Ma, Jing; Song, Guangchun; Thomas, Melvin E 3rd; Umeda, Masayuki; Maciaszek, Jamie L; Wong, Jasmine C; Wintering, Astrid; Wang, Lu; Emanuel, Peter D; Loh, Mignon L; Tasian, Sarah K; Stieglitz, Elliot; Schwartz, Jason R; Shannon, Kevin M; Klco, Jeffery M

In vivo validation of the palmitoylation cycle as a therapeutic target in NRAS-mutant cancer.

体内验证棕榈酰化循环作为 NRAS 突变癌症的治疗靶点

Decker Matthew, Huang Benjamin J, Ware Timothy, Boone Christopher, Tang Michelle, Ybarra Julia, Ballapuram Aishwarya C, Taran Katrine A, Chen Pan-Yu, Amendáriz Marcos, Leung Camille J, Harris Max, Tjoa Karensa, Hongo Henry, Abelson Sydney, Rivera Jose, Ngo Nhi, Herbst Dylan M, Suciu Radu M, Guijas Carlos, Sedighi Kimia, Andalis Taylor, Roche Elysia, Xie Boer, Liu Yunlong, Smith Catherine C, Stieglitz Elliot, Niphakis Micah J, Cravatt Benjamin F, Shannon Kevin

Multi-selective RAS(ON) Inhibition Targets Oncogenic RAS Mutations and Overcomes RAS/MAPK-Mediated Resistance to FLT3 and BCL2 Inhibitors in Acute Myeloid Leukemia.

多选择性 RAS(ON) 抑制靶向致癌 RAS 突变,克服急性髓系白血病中 RAS/MAPK 介导的对 FLT3 和 BCL2 抑制剂的耐药性

Popescu Bogdan, Jones Matthew F, Piao Madison, Tran Elaine, Koh Andrew, Lomeli Isabelle, Peretz Cheryl A C, Murad Natalia, Abelson Sydney, Morales Carolina, Rivera Jose M, Pikman Yana, Cheng Michael L, Logan Aaron C, Stieglitz Elliot, Smith Catherine C