日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV-Mediated Delivery of Plakophilin-2a Arrests Progression of Arrhythmogenic Right Ventricular Cardiomyopathy in Murine Hearts: Preclinical Evidence Supporting Gene Therapy in Humans

AAV介导的Plakophilin-2a递送可阻止小鼠心脏中致心律失常性右室心肌病的进展:支持人类基因治疗的临床前证据

van Opbergen, Chantal J M; Narayanan, Bitha; Sacramento, Chester B; Stiles, Katie M; Mishra, Vartika; Frenk, Esther; Ricks, David; Chen, Grace; Zhang, Mingliang; Yarabe, Paul; Schwartz, Jonathan; Delmar, Mario; Herzog, Chris D; Cerrone, Marina

Vectorized Human Antibody-Mediated Anti-Eosinophil Gene Therapy.

载体化人抗体介导的抗嗜酸性粒细胞基因治疗

Gioulvanidou Maria, Sarklioglu Selenay, Chen Xinlei, Lebedeva Irina V, Inalman Yeliz, Pohl Mary Ann, Bourne Lloyd, Andrew David, Lorenz Ivo C, Stiles Katie M, Pagovich Odelya E, Hackett Neil R, Kaminsky Stephen M, de Mulder Rougvie Miguel, Crystal Ronald G

Can gene therapy be used to prevent cancer? Gene therapy for aldehyde dehydrogenase 2 deficiency

基因疗法可以用于预防癌症吗?醛脱氢酶2缺乏症的基因疗法

Montel, Rachel A; Munoz-Zuluaga, Carlos; Stiles, Katie M; Crystal, Ronald G

Intrapleural Gene Therapy for Alpha-1 Antitrypsin Deficiency-Related Lung Disease

α1-抗胰蛋白酶缺乏相关肺病的胸膜内基因治疗

Stiles, Katie M; Sondhi, Dolan; Kaminsky, Stephen M; De, Bishnu P; Rosenberg, Jonathan B; Crystal, Ronald G

Role of TSPAN9 in Alphavirus Entry and Early Endosomes

TSPAN9在甲病毒入侵和早期内体中的作用

Stiles, Katie M; Kielian, Margaret

Genome-wide RNAi screen identifies novel host proteins required for alphavirus entry

全基因组RNAi筛选鉴定出甲病毒入侵所需的新型宿主蛋白

Ooi, Yaw Shin; Stiles, Katie M; Liu, Catherine Y; Taylor, Gwen M; Kielian, Margaret

Alphavirus entry: NRAMP leads the way

甲型病毒感染:NRAMP 引领潮流

Stiles, Katie M; Kielian, Margaret