日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Giroctocogene fitelparvovec gene therapy for severe hemophilia A: 104-week analysis of the phase 1/2 Alta study

用于治疗重度血友病A的Giroctocogene fitelparvovec基因疗法:1/2期Alta研究的104周分析

Leavitt, Andrew D; Konkle, Barbara A; Stine, Kimo C; Visweshwar, Nathan; Harrington, Thomas J; Giermasz, Adam; Arkin, Steven; Fang, Annie; Plonski, Frank; Yver, Anne; Ganne, Florence; Agathon, Delphine; Resa, Maria de Los Angeles; Tseng, Li-Jung; Di Russo, Gregory; Cockroft, Bettina M; Cao, Liching; Rupon, Jeremy

Nutlin-3 treatment spares cisplatin-induced inhibition of bone healing while maintaining osteosarcoma toxicity.

Nutlin-3 治疗可避免顺铂引起的骨愈合抑制,同时保持对骨肉瘤的毒性

Stine Kimo C, Wahl Elizabeth C, Liu Lichu, Skinner Robert A, VanderSchilden Jaclyn, Bunn Robert C, Montgomery Corey O, Aronson James, Becton David L, Nicholas Richard W, Swearingen Christopher J, Suva Larry J, Lumpkin Charles K

Dissecting the heterogeneity of macrophage activation syndrome

剖析巨噬细胞活化综合征的异质性

Hoepner, Robert; Faissner, Simon; Klasing, Anja; Schneider, Ruth; Metz, Imke; Bellenberg, Barbara; Lukas, Carsten; Altmeyer, Peter; Gold, Ralf; Chan, Andrew; Davì, Sergio; Minoia, Francesca; Horne, AnnaCarin; Bovis, Francesca; Demirkaya, Erkan; Akikusa, Jonathan; Ayaz, Nuray Aktay; Barone, Patrizia; Bica, Bianca; Bolt, Isabel; Breda, Luciana; Davidsone, Zane; De Cunto, Carmen; De Inocencio, Jaime; Enciso, Sandra; Gallizzi, Romina; Griffin, Thomas; Hennon, Teresa; Horneff, Gerd; Ioseliani, Maka; Jeng, Michael; Kapovic, Agneza Marja; Lattanzi, Bianca; Lipton, Jeffrey M; Magni-Manzoni, Silvia; Nassif, Clarissa; Rumba, Ingrida; Magalhaes, Claudia Saad; Al-Mayouf, Sulaiman; Sewairi, Wafaa Mohammed; Stine, Kimo C; Vougiouka, Olga; Weaver, Lehn; Zletni, Mabruka Ahmed; Ruperto, Nicola; Martini, Alberto; Cron, Randy Q; Ravelli, Angelo

Cardiomyopathy in children with Down syndrome treated for acute myeloid leukemia: a report from the Children's Oncology Group Study POG 9421

唐氏综合征患儿接受急性髓系白血病治疗后发生心肌病:儿童肿瘤协作组 POG 9421 研究报告

O'Brien, Maureen M; Taub, Jeffrey W; Chang, Myron N; Massey, Gita V; Stine, Kimo C; Raimondi, Susana C; Becton, David; Ravindranath, Yaddanapudi; Dahl, Gary V