日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Prenatal Intraportal Delivery of Polymeric Nanoparticles to Fetal Rhesus Monkeys (Macaca mulatta)

向恒河猴胎儿(Macaca mulatta)进行产前门静脉内聚合物纳米颗粒递送

Piotrowski-Daspit, Alexandra S; Lynn, Anna Y; Eaton, David A; Bracaglia, Laura G; Markey, Arianna I; Mortlock, Ryland D; Stitelman, David H; Martinez, Michele L; Lee, Charles C; Kliman, Harvey J; Glazer, Peter M; Tarantal, Alice F; Saltzman, W Mark

Systemic in utero gene editing as a treatment for cystic fibrosis

系统性子宫内基因编辑作为囊性纤维化的治疗方法

Ricciardi, Adele S; Barone, Christina; Putman, Rachael; Quijano, Elias; Gupta, Anisha; Nguyen, Richard; Mandl, Hanna; Piotrowski-Daspit, Alexandra S; Lopez-Giraldez, Francesc; Luks, Valerie; Freedman-Weiss, Mollie R; Farrelly, James; Ahle, Samantha; Lynn, Anna Y; Glazer, Peter M; Saltzman, W Mark; Stitelman, David H; Egan, Marie E

Altered Epithelial-Mesenchymal Progenitor States Lead to Matrix Deposition, Tissue Inflammation, and Transitional Epithelial State in Congenital Diaphragmatic Hernia

先天性膈疝中上皮-间质祖细胞状态的改变导致基质沉积、组织炎症和移行上皮状态的形成

Rivero, Rachel; Edelstein, Sophie; Haynes, Connor; Mizoguchi, Satoshi; Wang, Nuoya; Saltzman, Mark; Stitelman, David H; Raredon, Micha Sam Brickman

Biodistribution of Polymeric Nanoparticles following in utero Delivery to a Nonhuman Primate

聚合物纳米颗粒在子宫内输送至非人灵长类动物后的生物分布

Eaton, David A; Lynn, Anna Y; Surprenant, Juliana M; Deschenes, Emily I; Guerra, Mary Elizabeth; Rivero, Rachel; Yung, Nicholas K; O'Connor, Merissa; Glazer, Peter M; Bahtiyar, Mert Ozan; Saltzman, W Mark; Stitelman, David H

The technical and ethical framework of fetal therapy: past and current advances

胎儿治疗的技术和伦理框架:过去和现在的进展

Lynn, Anna Y; Glazer, Peter M; Saltzman, W Mark; Stitelman, David H

In utero delivery of miRNA induces epigenetic alterations and corrects pulmonary pathology in congenital diaphragmatic hernia

子宫内递送miRNA可诱导表观遗传改变并纠正先天性膈疝的肺部病理

Ullrich, Sarah J; Yung, Nicholas K; Bauer-Pisani, Tory J; Maassel, Nathan L; Guerra, Mary Elizabeth; Freedman-Weiss, Mollie; Ahle, Samantha L; Ricciardi, Adele S; Sauler, Maor; Saltzman, W Mark; Piotrowski-Daspit, Alexandra S; Stitelman, David H

Prenatal Somatic Cell Gene Therapies: Charting a Path Toward Clinical Applications (Proceedings of the CERSI-FDA Meeting)

产前体细胞基因疗法:规划临床应用之路(CERSI-FDA会议论文集)

Herzeg, Akos; Almeida-Porada, Graça; Charo, R Alta; David, Anna L; Gonzalez-Velez, Juan; Gupta, Nalin; Lapteva, Larissa; Lianoglou, Billie; Peranteau, William; Porada, Christopher; Sanders, Stephan J; Sparks, Teresa N; Stitelman, David H; Struble, Evi; Sumner, Charlotte J; MacKenzie, Tippi C

Nanoparticles for delivery of agents to fetal lungs

用于向胎儿肺部输送药物的纳米颗粒

Ullrich, Sarah J; Freedman-Weiss, Mollie; Ahle, Samantha; Mandl, Hanna K; Piotrowski-Daspit, Alexandra S; Roberts, Katherine; Yung, Nicholas; Maassel, Nathan; Bauer-Pisani, Tory; Ricciardi, Adele S; Egan, Marie E; Glazer, Peter M; Saltzman, W Mark; Stitelman, David H

In utero nanoparticle delivery for site-specific genome editing

利用纳米颗粒在子宫内进行位点特异性基因组编辑

Ricciardi, Adele S; Bahal, Raman; Farrelly, James S; Quijano, Elias; Bianchi, Anthony H; Luks, Valerie L; Putman, Rachael; López-Giráldez, Francesc; Coşkun, Süleyman; Song, Eric; Liu, Yanfeng; Hsieh, Wei-Che; Ly, Danith H; Stitelman, David H; Glazer, Peter M; Saltzman, W Mark

Life-Long Transgene Expression in Skeletal Muscle Without Transduction of Satellite Cells Following Embryonic Myogenic Progenitor Transduction by Lentivirus Administered in Utero.

通过子宫内注射慢病毒对胚胎成肌祖细胞进行转导,无需转导卫星细胞即可在骨骼肌中实现终身转基因表达

Stitelman David H, Brazelton Tim R, Endo Masayuki, Bora Archana, Traas Jeremy, Zoltick Philip W, Flake Alan W