日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Discovering metabolic disease gene interactions by correlated effects on cellular morphology

通过对细胞形态的相关影响发现代谢疾病基因相互作用

Yang Jiao, Umer Ahmed, M F Michelle Sim, Andrea Bejar, Xiaolan Zhang, M Mesbah Uddin Talukder, Robert Rice, Jason Flannick, Anna I Podgornaia, Dermot F Reilly, Jesse M Engreitz, Maria Kost-Alimova, Kate Hartland, Josep-Maria Mercader, Sara Georges, Vilas Wagh, Marija Tadin-Strapps, John G Doench, J

TMEM175 deficiency impairs lysosomal and mitochondrial function and increases α-synuclein aggregation

TMEM175 缺乏会损害溶酶体和线粒体功能并增加 α-突触核蛋白聚集

Sarah Jinn, Robert E Drolet, Paige E Cramer, Andus Hon-Kit Wong, Dawn M Toolan, Cheryl A Gretzula, Bhavya Voleti, Galya Vassileva, Jyoti Disa, Marija Tadin-Strapps, David J Stone

Silencing Myostatin Using Cholesterol-conjugated siRNAs Induces Muscle Growth

利用胆固醇偶联的siRNA沉默肌肉生长抑制素可诱导肌肉生长

Khan, Tayeba; Weber, Hans; DiMuzio, Jillian; Matter, Andrea; Dogdas, Belma; Shah, Tosha; Thankappan, Anil; Disa, Jyoti; Jadhav, Vasant; Lubbers, Laura; Sepp-Lorenzino, Laura; Strapps, Walter R; Tadin-Strapps, Marija

Dose-dependent effects of siRNA-mediated inhibition of SCAP on PCSK9, LDLR, and plasma lipids in mouse and rhesus monkey

siRNA 介导的 SCAP 抑制对小鼠和恒河猴 PCSK9、LDLR 和血浆脂质的剂量依赖性影响

Kristian K Jensen, Marija Tadin-Strapps, Sheng-Ping Wang, James Hubert, Yanqing Kan, Yong Ma, David G McLaren, Stephen F Previs, Kithsiri B Herath, Ablatt Mahsut, Andy Liaw, Shubing Wang, Steven J Stout, CarolAnn Keohan, Gail Forrest, David Coelho, Satya Yendluri, Stephanie Williams, Martin Koser, S

Preclinical and translational evaluation of coagulation factor IXa as a novel therapeutic target

凝血因子 IXa 作为新型治疗靶点的临床前和转化评估

Wendy Ankrom, Harold B Wood, Jiayi Xu, Wayne Geissler, Tom Bateman, Manash S Chatterjee, Kung-I Feng, Joseph M Metzger, Walter R Strapps, Marija Tadin-Strapps, Dietmar Seiffert, Patrick Andre

Proof-of-concept Studies for siRNA-mediated Gene Silencing for Coagulation Factors in Rat and Rabbit

大鼠和兔凝血因子siRNA介导基因沉默的概念验证研究

Chen, Zhu; Luo, Bin; Cai, Tian-Quan; Thankappan, Anil; Xu, Yiming; Wu, Weizhen; DiMuzio, Jillian; Lifsted, Traci; DiPietro, Marty; Disa, Jyoti; Ng, Bruce; Leander, Karen; Clark, Seth; Hoos, Lizbeth; Zhou, Yuchen; Jochnowitz, Nina; Jachec, Christine; Szczerba, Peter; Gindy, Marian E; Strapps, Walter; Sepp-Lorenzino, Laura; Seiffert, Dietmar A; Lubbers, Laura; Tadin-Strapps, Marija

Mutations in the cholesterol transporter gene ABCA5 are associated with excessive hair overgrowth

胆固醇转运蛋白基因 ABCA5 的突变与毛发过度生长有关

Gina M DeStefano, Mazen Kurban, Kwame Anyane-Yeboa, Claudia Dall'Armi, Gilbert Di Paolo, Heather Feenstra, Nanette Silverberg, Luis Rohena, Larissa D López-Cepeda, Vaidehi Jobanputra, Katherine A Fantauzzo, Maija Kiuru, Marija Tadin-Strapps, Antonio Sobrino, Anna Vitebsky, Dorothy Warburton, Brynn L

Pharmacological Characterization of a Novel ENaCα siRNA (GSK2225745) With Potential for the Treatment of Cystic Fibrosis

新型ENaCα siRNA (GSK2225745) 的药理学特征及其在囊性纤维化治疗中的应用潜力

Clark, Kenneth L; Hughes, Stephen A; Bulsara, Pallav; Coates, Jill; Moores, Kitty; Parry, Joel; Carr, Michael; Mayer, Ruth J; Wilson, Paul; Gruenloh, Chris; Levin, Daren; Darton, Jill; Weber, Wolf-Michael; Sobczak, Katja; Gill, Deborah R; Hyde, Stephen C; Davies, Lee A; Pringle, Ian A; Sumner-Jones, Stephanie G; Jadhav, Vasant; Jamison, Sharon; Strapps, Walter R; Pickering, Victoria; Edbrooke, Mark R

Rescue of Mtp siRNA-induced hepatic steatosis by DGAT2 siRNA silencing.

通过DGAT2 siRNA沉默挽救Mtp siRNA诱导的肝脂肪变性

Tep Samnang, Mihaila Radu, Freeman Alexander, Pickering Victoria, Huynh Felicia, Tadin-Strapps Marija, Stracks Allison, Hubbard Brian, Caldwell Jeremy, Flanagan W Michael, Kuklin Nelly A, Ason Brandon

siRNA-induced liver ApoB knockdown lowers serum LDL-cholesterol in a mouse model with human-like serum lipids

在具有类似人类血清脂质的小鼠模型中,siRNA诱导的肝脏ApoB敲低降低了血清LDL胆固醇水平。

Marija Tadin-Strapps ,Laurence B Peterson ,Anne-Marie Cumiskey ,Raymond L Rosa ,Vivienne Halili Mendoza ,Jose Castro-Perez ,Oscar Puig ,Liwen Zhang ,Walter R Strapps ,Satyasri Yendluri ,Lori Andrews ,Victoria Pickering ,Julie Rice ,Lily Luo ,Zhu Chen ,Samnang Tep ,Brandon Ason ,Elizabeth Polizzi Somers ,Alan B Sachs ,Steven R Bartz ,Jenny Tian ,Jayne Chin ,Brian K Hubbard ,Kenny K Wong ,Lyndon J Mitnaul