日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Systemic immune challenge exacerbates neurodegeneration in a model of neurological lysosomal disease

系统性免疫挑战加剧了神经溶酶体疾病模型中的神经退行性

Oriana Mandolfo, Helen Parker, Èlia Aguado, Yuko Ishikawa Learmonth, Ai Yin Liao, Claire O'Leary, Stuart Ellison, Gabriella Forte, Jessica Taylor, Shaun Wood, Rachel Searle, Rebecca J Holley, Hervé Boutin, Brian W Bigger

Design and validation of a GMP stem cell manufacturing protocol for MPSII hematopoietic stem cell gene therapy

MPSII造血干细胞基因治疗的GMP干细胞生产方案的设计和验证

Stuart Ellison, Karen Buckland, Yuko Learmonth, Victoria Day, Spandan Kalra, Lauren Howe, Francisco José Roman-Rodriguez, Jose Bonafont, Laura Booth, Rebecca Holley, Jon Smythe, Simon Jones, Adrian Thrasher, Claire Booth, Brian W Bigger

Sustained long-term disease correction in a murine model of MPSII following stem cell gene therapy

干细胞基因治疗后,小鼠 MPSII 模型的疾病得到长期持续矫正

Stuart Ellison, Aiyin Liao, Hélène F E Gleitz, Helen Parker, Laura Booth, John Robinson, Shaun Wood, Jessica Taylor, Rebecca Holley, Brian W Bigger

Actinomycin D downregulates Sox2 and improves survival in preclinical models of recurrent glioblastoma

放线菌素 D 下调 Sox2 并提高复发性胶质母细胞瘤临床前模型的生存率

Jessica T Taylor, Stuart Ellison, Alina Pandele, Shaun Wood, Erica Nathan, Gabriella Forte, Helen Parker, Egor Zindy, Mark Elvin, Alan Dickson, Kaye J Williams, Konstantina Karabatsou, Martin McCabe, Catherine McBain, Brian W Bigger