Gene Augmentation and Readthrough Rescue Channelopathy in an iPSC-RPE Model of Congenital Blindness
基因增强和通读挽救了iPSC-RPE先天性失明模型中的通道病
期刊:American Journal of Human Genetics
影响因子:8.1
doi:10.1016/j.ajhg.2018.12.019
Shahi, Pawan K; Hermans, Dalton; Sinha, Divya; Brar, Simran; Moulton, Hannah; Stulo, Sabrina; Borys, Katarzyna D; Capowski, Elizabeth; Pillers, De-Ann M; Gamm, David M; Pattnaik, Bikash R