Pharmacological enhancement of KCC2 gene expression exerts therapeutic effects on human Rett syndrome neurons and Mecp2 mutant mice
药理学方法增强KCC2基因表达对人类雷特综合征神经元和Mecp2突变小鼠具有治疗作用。
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.aau0164
Tang, Xin; Drotar, Jesse; Li, Keji; Clairmont, Cullen D; Brumm, Anna Sophie; Sullins, Austin J; Wu, Hao; Liu, Xiaoxiao Shawn; Wang, Jinhua; Gray, Nathanael S; Sur, Mriganka; Jaenisch, Rudolf
