Recombinant SMN protein synergizes with spinal muscular atrophy therapy to counteract pathological motor neuron phenotypes
重组SMN蛋白与脊髓性肌萎缩症疗法协同作用,对抗病理性运动神经元表型
期刊:Translational Neurodegeneration
影响因子:15.2
doi:10.1186/s40035-024-00455-4
Brambilla, Liliana; Valori, Chiara F; Guidotti, Giulia; Martorana, Francesca; Sulmona, Claudia; De Martini, Lisa Benedetta; Canciani, Anselmo; Fumagalli, Marco; Talpo, Francesca; Biella, Gerardo; Di Pasquale, Elisa; Iacobucci, Claudio; Forneris, Federico; Zhou, Haiyan; Rossi, Daniela