日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis

为首次在囊性纤维化患者中开展慢病毒人体试验做准备

Alton, Eric W F W; Beekman, Jeffery M; Boyd, A Christopher; Brand, June; Carlon, Marianne S; Connolly, Mary M; Chan, Mario; Conlon, Sinead; Davidson, Heather E; Davies, Jane C; Davies, Lee A; Dekkers, Johanna F; Doherty, Ann; Gea-Sorli, Sabrina; Gill, Deborah R; Griesenbach, Uta; Hasegawa, Mamoru; Higgins, Tracy E; Hironaka, Takashi; Hyndman, Laura; McLachlan, Gerry; Inoue, Makoto; Hyde, Stephen C; Innes, J Alastair; Maher, Toby M; Moran, Caroline; Meng, Cuixiang; Paul-Smith, Michael C; Pringle, Ian A; Pytel, Kamila M; Rodriguez-Martinez, Andrea; Schmidt, Alexander C; Stevenson, Barbara J; Sumner-Jones, Stephanie G; Toshner, Richard; Tsugumine, Shu; Wasowicz, Marguerite W; Zhu, Jie

Pharmacological Characterization of a Novel ENaCα siRNA (GSK2225745) With Potential for the Treatment of Cystic Fibrosis

新型ENaCα siRNA (GSK2225745) 的药理学特征及其在囊性纤维化治疗中的应用潜力

Clark, Kenneth L; Hughes, Stephen A; Bulsara, Pallav; Coates, Jill; Moores, Kitty; Parry, Joel; Carr, Michael; Mayer, Ruth J; Wilson, Paul; Gruenloh, Chris; Levin, Daren; Darton, Jill; Weber, Wolf-Michael; Sobczak, Katja; Gill, Deborah R; Hyde, Stephen C; Davies, Lee A; Pringle, Ian A; Sumner-Jones, Stephanie G; Jadhav, Vasant; Jamison, Sharon; Strapps, Walter R; Pickering, Victoria; Edbrooke, Mark R

The use of carboxymethylcellulose gel to increase non-viral gene transfer in mouse airways

使用羧甲基纤维素凝胶增加小鼠气道中的非病毒基因转移

Uta Griesenbach, Cuixiang Meng, Raymond Farley, Marguerite Y Wasowicz, Felix M Munkonge, Mario Chan, Charlotte Stoneham, Stephanie G Sumner-Jones, Ian A Pringle, Deborah R Gill, Stephen C Hyde, Barbara Stevenson, Emma Holder, Hiroshi Ban, Mamoru Hasegawa, Seng H Cheng, Ronald K Scheule, Patrick L Si

Gene therapy for cystic fibrosis lung disease

囊性纤维化肺病的基因疗法

Wells, Timothy S; Bhattarai, Gandhi R; Hawkins, Kevin; Cheng, Yan; Ruiz, Joann; Barnowski, Cynthia A; Spivack, Barney; Yeh, Charlotte S; Sumner-Jones, Stephanie G; Gill, Deborah R; Hyde, Stephen C