Whole-transcriptome sequencing in neural and non-neural tissues of a mouse model identifies miR-34a as a key regulator in SMA pathogenesis
对小鼠模型神经和非神经组织进行全转录组测序,发现 miR-34a 是 SMA 发病机制中的关键调控因子。
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102490
Wu, Liucheng; Sun, Junjie; Wang, Li; Chen, Zhiheng; Guan, Zeyuan; Du, Lili; Qu, Ruobing; Liu, Chun; Shao, Yixiang; Hua, Yimin