日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial

marstacimab预防治疗A/B型血友病伴抑制剂的疗效和安全性:来自3期BASIS试验的结果

Matino, Davide; Acharya, Suchitra S; Taylor, Carrie Turich; Sun, Pengling; Agathon, Delphine; Raje, Sangeeta; Gould, Travis; Palladino, Andrew; Mahlangu, Johnny; Lissitchkov, Toshko; Todorova, Mariya; Chan, Anthony; Carcao, Manuel; Sun, Jing; Yang, Renchi; Wu, Runhui; Jin, Chenghao; Zeng, Xiaojing; Boban, Ana; Bilic, Ernest; Frenzel, Laurent; Fung Chan, Godfrey Chi; Kong Li, Chi; Apte, Shashikant; Choraria, Nirmalkumar; Chistolini, Antonio; Marchesini, Emanuela; Peyvandi, Flora; Fujii, Teruhisa; Matsushita, Tadashi; Kaneda, Makoto; Lyu, Chuhl Joo; Park, Young Shil; Kim, SungEun; Martinez, Laura Villarreal; Adrian, Javier Morales; Wali, Yasser; Al Khabori, Murtadha; Kurtov, Igor; Alzahrani, Hazzaa; Zaher, Galila; Micic, Dragan; Miljic, Predrag; Kostic, Gordana; Vucic, Miodrag; Djurdjevic, Predrag; Hidalgo, Olga Benitez; Porras, Jose Gonzalez; Jiménez-Yuste, Víctor; Calvo Villas, Jose Manuel; Lopez Fernandez, Maria Fernanda; Albayrak, Canan; Okan, Vahap; Balkan, Can; Sahin, Fahri; Antmen, Ali; Unal, Ekrem; Visweshwar, Nathan; Sharathkumar, Anjali; Kruse-Jarres, Rebecca

Evaluation of Mitochondrial Complex 1 Density with [(18)F]BCPP-EF in a Murine Model and Individuals with Friedreich Ataxia.

利用 [(18)F]BCPP-EF 对小鼠模型和弗里德赖希共济失调患者进行线粒体复合物 1 密度评估

Chen Laigao, Rizzo Gaia, Bulawa Christine, Van Dijk Koene R A, Henning Erica C, Martelli Alain, Palmer Jeffrey, McIntosh Avery, Pregel Marko, Sun Pengling, Adewunmi Emmanuel, Aldridge Mark, Chan Jackson, Gunn Roger N, Huiban Mickael, Listanco Allan, Loudon Peter T, Moz Sara, Passchier Jan, Sauvage Lauren, Stewart Rachel, Wells Lisa, Rabiner Eugenii A, Charnas Lawrence R, Festenstein Richard J

A phase 1b/2 clinical study of marstacimab, targeting human tissue factor pathway inhibitor, in haemophilia

一项针对人组织因子途径抑制剂的marstacimab治疗血友病的1b/2期临床研究

Mahlangu, Johnny N; Lamas, Jose Luis; Morales, Juan Cristobal; Malan, Daniel R; Šalek, Silva Zupančić; Wang, Michael; Boggio, Lisa N; Hegemann, Inga; Mital, Andrzej; Cardinal, Matthew; Zhu, Tong; Sun, Pengling; Arkin, Steven