日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Human promoter-driven AAV tools enable precision gene therapy targeting cochlear hair cells

人源启动子驱动的腺相关病毒(AAV)工具可实现针对耳蜗毛细胞的精准基因治疗。

Zhang, Liyan; Lu, Yicheng; Wu, Xianmin; Fan, Jinyi; Zhang, Xinru; Xu, Yang; Wei, Hao; Sun, Qiuhan; Jiang, Lulu; Tuo, Huawei; Li, Nianci; Jin, Hua; Cao, Wu; Ye, Beibei; Zhang, Ziyu; Zhang, Yunkai; Chen, Fangyi; Lu, Ling; Qi, Jieyu; Chai, Renjie; Tan, Fangzhi

Optimized in vivo base editing restores auditory function in a DFNA15 mouse model

优化的体内碱基编辑可恢复DFNA15小鼠模型的听觉功能

Wang, Man; Zhang, Ziyu; Wang, Xiaohan; Zhang, Liyan; Chen, Xiangyan; Li, Nianci; Sun, Qiuhan; Lu, Yicheng; He, Zuhong; Yang, Hongbo; Tan, Fangzhi; Qi, Jieyu; Chai, Renjie

Correction to "AAV-Mediated Gene Cocktails Enhance Supporting Cell Reprogramming and Hair Cell Regeneration"

更正“AAV介导的基因混合物增强支持细胞重编程和毛发细胞再生”

Zhang, Liyan; Chen, Xin; Wang, Xinlin; Zhou, Yinyi; Fang, Yuan; Gu, Xingliang; Zhang, Ziyu; Sun, Qiuhan; Li, Nianci; Xu, Lei; Tan, Fangzhi; Chai, Renjie; Qi, Jieyu

AAV-Sparcl1 promotes hair cell regeneration by increasing supporting cell plasticity

AAV-Sparcl1通过增加支持细胞可塑性来促进毛细胞再生

Li, Nianci; Tan, Fangzhi; Zhang, Liyan; Ding, Xiaoqiong; Sun, Qiuhan; Wang, Man; Zhang, Ziyu; Lu, Yicheng; Zhou, Yinyi; Qian, Xiaoyun; Ye, Fanglei; Qi, Jieyu; Chai, Renjie

Combined AAV-mediated specific Gjb2 expression restores hearing in DFNB1 mouse models.

联合 AAV 介导的特异性 Gjb2 表达可恢复 DFNB1 小鼠模型的听力

Sun Qiuhan, Tan Fangzhi, Zhang Liyan, Lu Yicheng, Wei Hao, Li Nianci, Jiang Lulu, Zhou Yinyi, Chen Tian, Lu Ling, Li Geng-Lin, Qi Jieyu, Yang Shiming, Chai Renjie

Current AAV-mediated gene therapy in sensorineural hearing loss

目前,AAV介导的基因疗法在感音神经性听力损失中的应用

Qi, Jieyu; Fu, Xiaolong; Zhang, Liyan; Tan, Fangzhi; Li, Nianci; Sun, Qiuhan; Hu, Xiaojie; He, Zuhong; Xia, Ming; Chai, Renjie