Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency
腺苷脱氨酶严重联合免疫缺陷症基因治疗后的长期结果
期刊:Blood
影响因子:21
doi:10.1182/blood.2020010260
Bryanna Reinhardt, Omar Habib, Kit L Shaw, Elizabeth Garabedian, Denise A Carbonaro-Sarracino, Dayna Terrazas, Beatriz Campo Fernandez, Satiro De Oliveira, Theodore B Moore, Alan K Ikeda, Barbara C Engel, Gregory M Podsakoff, Roger P Hollis, Augustine Fernandes, Connie Jackson, Sally Shupien, Suparn