Efficacious Androgen Hormone Administration in Combination with Adeno-Associated Virus Vector-Mediated Gene Therapy in Female Mice with Pompe Disease
在患有庞贝氏病的雌性小鼠中，有效的雄激素激素给药联合腺相关病毒载体介导的基因治疗
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2021.218
Han, Sang-Oh; Gheorghiu, Dorothy; Chang, Alex; Mapatano, Sweet Hope; Li, Songtao; Brooks, Elizabeth; Koeberl, Dwight
