日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry

Ravulizumab治疗阵发性睡眠性血红蛋白尿症患者的真实世界疗效和安全性:来自国际PNH注册研究的证据

Röth, Alexander; Patriquin, Christopher J; Szer, Jeff; Terriou, Louis; Patel, Ami S; Metzger, Jesse; Gustovic, Philippe; Nishimura, Jun-Ichi; Brodsky, Robert A

Interferon-α Nasal Spray Prophylaxis Reduces COVID-19 in Cancer Patients: A Randomized, Double-Blinded, Placebo-Controlled Trial.

干扰素-α鼻喷雾剂预防可降低癌症患者的COVID-19感染率:一项随机、双盲、安慰剂对照试验。

Yong Michelle K, Thursky Karin, Crane Megan, Spelman Tim, Mahar Robert K, Simpson Julie A, Scott Andrew M, Harrison Simon J, Szer Jeff, Pellegrini Marc, Lingaratnam Senthil, Pang Ken C, Tennakoon Surekha, Sim Beatrice Z, Blyth Emily, Gan Hui K, Quach Hang, McIntosh Michelle P, Page Hayley, Woolstencroft Rachel, Slavin Monica

Ruxolitinib Versus Best Available Therapy in Patients With Steroid-Refractory Acute Graft-Versus-Host Disease: Final Analysis From the Randomized Phase III REACH2 Trial

鲁索替尼与现有最佳疗法治疗类固醇难治性急性移植物抗宿主病患者的疗效比较:随机III期REACH2试验的最终分析

Mohty, Mohamad; Socié, Gerard; Szer, Jeff; Niederwieser, Dietger; Butler, Jason; Wagner-Drouet, Eva; Or, Reuven; Rovenvald-Zuckerman, Tsila; Bozdag, Sinem Civriz; Forcade, Edouard; Grillo, Giovanni; Kröger, Nicolaus; Stölzel, Friedrich; Russo, Domenico; Sanz, Jaime; Sarkar, Rajendra; Stefanelli, Tommaso; Wilke, Celine; Zeiser, Robert; von Bubnoff, Nikolas

Cytotoxic lymphocyte effector function is unaffected in patients with Gaucher disease

戈谢病患者的细胞毒性淋巴细胞效应功能不受影响。

Jinyun Zou ,Tahereh Noori ,Mark Walterfang ,Jeff Szer ,Joseph A Trapani ,Ilia Voskoboinik

Preimplantation Genetic Testing (PGT) to Reduce the Risk for GBA-Related Parkinson's Disease: Expanding the Applications for Embryo Selection

胚胎植入前遗传学检测(PGT)降低GBA相关帕金森病风险:拓展胚胎选择的应用

Zuckerman, Shachar; Zimran, Ari; Szer, Jeff; Revel-Vilk, Shoshana; Altarescu, Gheona

Ravulizumab demonstrates long-term efficacy, safety and favorable patient survival in patients with paroxysmal nocturnal hemoglobinuria

Ravulizumab 在阵发性睡眠性血红蛋白尿症患者中显示出长期疗效、安全性和良好的患者生存率。

Kulasekararaj, Austin; Brodsky, Robert; Schrezenmeier, Hubert; Griffin, Morag; Röth, Alexander; Piatek, Caroline; Ogawa, Masayo; Yu, Ji; Patel, Ami S; Patel, Yogesh; Notaro, Rosario; Usuki, Kensuke; Kulagin, Alexander; Gualandro, Sandra; Füreder, Wolfgang; Peffault de Latour, Regis; Szer, Jeff; Lee, Jong Wook

Anchored Indirect Treatment Comparison Finds Comparable Effects of Pegcetacoplan and Iptacopan in Paroxysmal Nocturnal Haemoglobinuria

锚定间接治疗比较研究发现,在阵发性睡眠性血红蛋白尿症中,培塞他考普兰和伊普他考潘的疗效相当

de Latour, Regis Peffault; Kulasekararaj, Austin; Dingli, David; Wilson, Koo; Wojciechowski, Piotr; Hakimi, Zalmai; Nazir, Jameel; Czech, Barbara; Hillmen, Peter; Szer, Jeff

Hyperuricaemia in type 1 Gaucher disease: is uric acid a biomarker for disease severity?

型戈谢病中的高尿酸血症:尿酸是疾病严重程度的生物标志物吗?

Hexner-Erlichman, Zufit; Watad, Salmas; Szer, Jeff; Habashi, Nayaf; Rosenbaum, Hanna

Incidence and Clinical Outcomes of Multiple Viral Infections After Allogeneic Hematopoietic Cell Transplantation

异基因造血干细胞移植后多种病毒感染的发生率和临床结局

Yong, Kar Yee; Tio, Shio Yen; Sim, Beatrice Z; Sasadeusz, Joe; Rivalland, Alex; Chee, Lynette; Szer, Jeff; Spelman, Tim; Slavin, Monica; Ritchie, David; Yong, Michelle K

Continuous and differential improvement in worldwide access to hematopoietic cell transplantation: activity has doubled in a decade with a notable increase in unrelated and non-identical related donors

全球造血干细胞移植的可及性持续且差异化地提高:十年来,移植数量翻了一番,其中非亲缘供者和非同胞供者的数量显著增加。

Atsuta, Yoshiko; Baldomero, Helen; Neumann, Daniel; Sureda, Anna; DeVos, Jakob D; Iida, Minako; Karduss, Amado; Purtill, Duncan; Elhaddad, Alaa M; Bazuaye, Nosa G; Bonfim, Carmem; De la Camara, Rafael; Chaudhri, Naeem A; Ciceri, Fabio; Correa, Cinthya; Frutos, Cristobal; Galeano, Sebastian; Garderet, Laurent; Gonzalez-Ramella, Oscar; Greco, Raffaella; Hamad, Nada; Hazenberg, Mette D; Horowitz, Mary M; Kalwak, Krzysztof; Ko, Bor-Sheng; Kodera, Yoshihisa; Koh, Mickey Bc; Liu, Kaiyan; McLornan, Donal P; Moon, Joon Ho; Neven, Benedicte; Okamoto, Shinichiro; Pasquini, Marcelo C; Passweg, Jakob R; Paulson, Kristjan; Rondelli, Damiano; Ruggeri, Annalisa; Seber, Adriana; Snowden, John A; Srivastava, Alok; Szer, Jeff; Weisdorf, Daniel; Worel, Nina; Greinix, Hildegard; Saber, Wael; Aljurf, Mahmoud; Niederwieser, Dietger