A Prospective Natural History Study Protocol for Clinical Trial Readiness in Synaptic Disorders
突触疾病临床试验准备的前瞻性自然史研究方案
期刊:
影响因子:
doi:10.64898/2026.01.30.26344887
McKee, Jillian L; Ruggiero, Sarah M; Cunningham, Kristin; Coyne, JoeyLynn; McSalley, Ian; Kaufman, Michael C; Bane, Bintou; Chisari, Torrey; Toib, Jonathan; Glatts, Carlyn; Tefft, Sarah; Orlando, Julie M; Padmanabhan, Viveknarayanan; Gonzalez, Alexander K; Harrison, Alicia; Woo, Charlene; Zbikowski, Stephanie A; Dhaduk, Rency; Mercurio, Johanna; McCarthy, Macie; Magielski, Jan H; Grinspan, Zachary; Abbott, Megan; Knowles, Juliet; Chao, Hsiao-Tuan; Xiong, Katherine; Berry-Kravis, Elizabeth; Tabarestani, Sepideh; Graglia, J Michael; Helde, Kathryn; McNamar, Virginie; Rigby, Charlene Son; Goss, James; Demarest, Scott; Miele, Andrea; Prosser, Benjamin; Boland, Michael J; Pierce, Samuel R; Helbig, Ingo