日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Oral splicing modulator branaplam in Huntington's disease: a phase 2 randomized controlled trial

口服剪接调节剂布拉那普拉姆治疗亨廷顿病:一项 II 期随机对照试验

Borowsky, Beth; Ramos, Harry; Caputo, Angelika; Hartmann, Andreas; Faller, Thomas; Peters, Thomas; Sui, Yihan; Liu, Fonda; Meadowcroft, Mark; David, Olivier J; Laisney, Marc; Kinhikar, Arvind; Marder, Karen S; Tabrizi, Sarah J; Landwehrmeyer, G Bernhard; Leavitt, Blair R

Genetic therapies for neurological diseases

神经系统疾病的基因疗法

Rahim, Ahad A; Kurian, Manju A; Zhou, Haiyan; Ferguson, Ross; Tabrizi, Sarah J; Lignani, Gabriele; Aquilina, Kristian; Waddington, Simon N

Optimized Xanthenium Photocages with Fused Ring Systems for Photoactivated Chemotherapy and G Protein-Coupled Receptor Photopharmacology

用于光激活化疗和G蛋白偶联受体光药理学的具有稠合环系统的优化呫吨光笼

Molnár, Tibor Á; Kozma, Eszter; Benedikti, Anna; Holczer, Márk; Kormos, Attila; Gonda, Zsombor; Balde, Ákos; Pühringer, Selina; Handl, Verena; Bayer, Christian; Huber, Waltraud; Ghaffari-Tabrizi-Wizsy, Nassim; Waldherr, Linda; Németh, Krisztina; Bojtár, Márton

Discovery of disrupted sustained attention and altered functional connectivity in far-from-onset Huntington's disease gene-expanded young adults

在亨廷顿病基因扩增的远期青年人中发现持续注意力受损和功能连接改变

Langley, Christelle; Leocadi, Michela; Hobbs, Nicola Z; Farag, Mena; Murphy, Michael J; Fayer, Kate; Scahill, Rachael I; Rowe, James B; Robbins, Trevor W; Tabrizi, Sarah J; Sahakian, Barbara J

Reactivation of the silenced BASP1 gene suppresses oncogenic WNT signaling in human colorectal cancer cells

沉默的BASP1基因的重新激活可抑制人结直肠癌细胞中的致癌WNT信号通路。

Weber, Leonie I; Timpen, Lea E; Egger-Hörschinger, Anna-Sophia; Schöpf, Philemon; Ayhan, Nesin D; Demmel, David; Hotze, Madlen; Zhang, Yang; Mehrabi, Mahdi; Puglisi, Kane; Stefan, Eduard; Ghaffari-Tabrizi-Wizsy, Nassim; Ramos-Pittol, José M; Kwiatkowski, Marcel; Hartl, Markus

Cerebrospinal Fluid Proenkephalin Predicts Striatal Atrophy Decades before Clinical Motor Diagnosis in Huntington's Disease

脑脊液中前脑啡肽水平可预测亨廷顿病患者纹状体萎缩,且早于临床运动症状的诊断数十年。

Farag, Mena; Murphy, Michael J; Hobbs, Nicola Z; Leocadi, Michela; Fayer, Kate; Thackeray, Olivia; Gobom, Johan; Ciosi, Marc; Heslegrave, Amanda; Zetterberg, Henrik; Langbehn, Douglas R; Monckton, Darren G; Wild, Edward J; Tabrizi, Sarah J; Scahill, Rachael I

Role of histone deacetylases and sirtuins in the ischaemic stroke: a systematic review and meta-analysis of animal studies

组蛋白去乙酰化酶和sirtuins在缺血性卒中中的作用:动物研究的系统评价和荟萃分析

Majdi, Ali; Yaraghi, Shahin; Moharrami, Ali; Ghaffari Tabrizi, Amirreza; Dojahani, Morteza; Alirezapour, Erfan; Mansori, Kamyar; Eskandari, Mehdi; Mostafavi, Hossein

Neoadjuvant Therapy for Esophageal Cancer

食管癌新辅助治疗

Samadzadeh Tabrizi, Nika; Marthy, Andrew; Fabian, Thomas

Pannexin 1a regulates visual system development and ocular integrity in zebrafish

Pannexin 1a 调控斑马鱼的视觉系统发育和眼部完整性

Sabour, Shiva; Houshangi-Tabrizi, Sarah; Zoidl, Georg S O; Zoidl, Georg R; Tabatabaei, Nima

Complementary metal-oxide-semiconductor (CMOS) time of evaporation measurement system for binary chemical monitoring

用于二元化学监测的互补金属氧化物半导体(CMOS)蒸发时间测量系统

Ghafar-Zadeh, Ebrahim; Forouhi, Saghi; Osouli Tabrizi, Hamed; Panahi, Abbas; Tahernezhad, Yasaman; Amrollahi Biyouki, Azadeh