日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Elevated Serum Concentrations of Lacosamide and Perampanel in a Pediatric Patient Following Coadministration of Clarithromycin for Mycoplasma pneumoniae Pneumonia

儿童患者在接受克拉霉素治疗肺炎支原体肺炎后,血清中拉考沙胺和吡仑帕奈的浓度升高

Meguro, Shotaro; Imai, Toru; Ishii, Wakako; Momoki, Emiko; Kawaguchi, Tadayasu; Matsuda, Kengo; Watanabe, Shintaro; Ootsuka, Susumu

A randomized phase I study of the safety and pharmacokinetics of BI 1291583 in healthy Japanese male subjects

一项随机 I 期研究,旨在评估 BI 1291583 在健康日本男性受试者中的安全性和药代动力学。

Tadayasu, Yusuke; Sarubbi, Donald; Furuichi, Takumi; Eleftheraki, Anastasia; Nakamura, Shuhei; Sauter, Wiebke; Hanada, Ryuzo

Evaluation of GLA variants detected in newborn screening for Fabry disease using biomarker analysis

利用生物标志物分析评估新生儿法布里病筛查中检测到的GLA变异体

Sawada, Takaaki; Kido, Jun; Tsukimura, Takahiro; Sugawara, Keishin; Shiga, Tomoko; Saito, Seiji; Togawa, Tadayasu; Inoue, Takahito; Watanabe, Yoriko; Hamada, Junpei; Sakuraba, Hitoshi; Nakamura, Kimitoshi

A Pediatric Case of Hypokalemic Periodic Paralysis With Fatigue and Myalgia

一例伴有疲劳和肌痛的低钾性周期性麻痹儿科病例报告

Horie, Mio; Fuchigami, Tatsuo; Kawaguchi, Tadayasu; Ishige, Mika; Morioka, Ichiro

Comparative study on incorporation of three recombinant human α-galactosidase A drugs (agalsidases) into cultured fibroblasts and organs/tissues of Fabry mice

三种重组人 α-半乳糖苷酶 A 药物(阿加糖苷酶)与法布里病小鼠培养成纤维细胞和器官/组织结合的比较研究

Takahiro Tsukimura, Tomoko Shiga, Tadayasu Togawa, Hitoshi Sakuraba

Does administration of hydroxychloroquine/amiodarone affect the efficacy of enzyme replacement therapy for Fabry mice?

羟氯喹/胺碘酮的使用是否会影响法布里小鼠酶替代疗法的疗效?

Takahiro Tsukimura, Koki Saito, Tomoko Shiga, Yasuhiro Ogawa, Hitoshi Sakuraba, Tadayasu Togawa

Profiles of Globotriaosylsphingosine Analogs and Globotriaosylceramide Isoforms Accumulated in Body Fluids from Various Phenotypic Fabry Patients

不同表型法布里病患者体液中积累的球状三己糖鞘氨醇类似物和球状三己糖神经酰胺同工型的分析

Shiga, Tomoko; Tsukimura, Takahiro; Kubota, Takao; Togawa, Tadayasu; Sakuraba, Hitoshi

Effects of switching from agalsidase-α to agalsidase-β on biomarkers, renal and cardiac parameters, and disease severity in fabry disease forming neutralizing antidrug antibodies: a case report

阿加糖酶-α 换用阿加糖酶-β 对法布里病患者生物标志物、肾脏和心脏参数以及疾病严重程度的影响:一例中和抗药抗体的病例报告

Shima, Hisato; Tsukimura, Takahiro; Shiga, Tomoko; Togawa, Tadayasu; Sakuraba, Hitoshi; Doi, Toshio; Ikeda, Yuka; Okamoto, Takuya; Yoshikawa, Yukari; Kimura, Takehiko; Iwase, Takashi; Inoue, Tomoko; Tashiro, Manabu; Okada, Kazuyoshi; Minakuchi, Jun

In Vivo Delivery of Therapeutic Molecules by Transplantation of Genome-Edited Induced Pluripotent Stem Cells

通过移植基因组编辑的诱导性多能干细胞进行体内治疗分子递送

Ittetsu Nakajima, Takahiro Tsukimura, Terumi Ono, Tomoko Shiga, Hiroshi Shitara, Tadayasu Togawa, Hitoshi Sakuraba, Yuichiro Miyaoka

Monitoring of anti-drug antibodies and disease-specific biomarkers in three patients from a Japanese Fabry family treated with enzyme replacement therapy

对接受酶替代疗法治疗的三名来自日本法布里病家族的患者进行抗药抗体和疾病特异性生物标志物监测

Kubota, Takao; Tsukimura, Takahiro; Shiga, Tomoko; Togawa, Tadayasu; Sakuraba, Hitoshi