Effects of switching from agalsidase-α to agalsidase-β on biomarkers, renal and cardiac parameters, and disease severity in fabry disease forming neutralizing antidrug antibodies: a case report
阿加糖酶-α 换用阿加糖酶-β 对法布里病患者生物标志物、肾脏和心脏参数以及疾病严重程度的影响:一例中和抗药抗体的病例报告
期刊:CEN Case Reports
影响因子:0.7
doi:10.1007/s13730-023-00843-1
Shima, Hisato; Tsukimura, Takahiro; Shiga, Tomoko; Togawa, Tadayasu; Sakuraba, Hitoshi; Doi, Toshio; Ikeda, Yuka; Okamoto, Takuya; Yoshikawa, Yukari; Kimura, Takehiko; Iwase, Takashi; Inoue, Tomoko; Tashiro, Manabu; Okada, Kazuyoshi; Minakuchi, Jun