Inability of α-cyclodextrins to accommodate cholesterol potentially underlies their lack of efficacy and ototoxicity in Niemann-Pick disease type C treatment
α-环糊精无法容纳胆固醇可能是其在治疗尼曼-匹克病C型时疗效不佳和具有耳毒性的潜在原因。
期刊:Scientific Reports
影响因子:3.9
doi:10.1038/s41598-025-15599-0
Yamada, Yusei; Tanaka, Mayuko; Ikeda, Yusei; Kondo, Yuki; Takeo, Toru; Nakagata, Naomi; Miwa, Toru; Takeda, Hiroki; Orita, Yorihisa; Motoyama, Keiichi; Higashi, Taishi; Arima, Hidetoshi; Seki, Takahiro; Kurauchi, Yuki; Katsuki, Hiroshi; Higaki, Katsumi; Matsusaka, Kotaro; Minami, Kentaro; Yoshikawa, Naoki; Ikeda, Ryuji; Matsuo, Muneaki; Irie, Tetsumi; Ishitsuka, Yoichi