AAV9-mediated gene supplementation therapy prevents and rescues arrhythmogenic cardiomyopathy in Pnpla2-mutated mice.
AAV9介导的基因补充疗法可预防和挽救Pnpla2突变小鼠的心律失常性心肌病
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.06.023
Zhang Xiulin, Wang Congrui, Chang Yuan, Jia Hao, Zhang Yue, Wang Yifan, Wang Weiteng, Han Han, Hu Yuhong, Shao Xijia, Wen Shuang, Tan Siyu, Zhang Ningning, Hua Xiumeng, Cui Hao, Chen Xiao, Song Jiangping