Mannose receptor-mediated delivery of moss-made α-galactosidase A efficiently corrects enzyme deficiency in Fabry mice
甘露糖受体介导的苔藓合成α-半乳糖苷酶A递送可有效纠正法布里病小鼠的酶缺乏症。
期刊:Journal of Inherited Metabolic Disease
影响因子:3.8
doi:10.1007/s10545-015-9886-9
Shen, Jin-Song; Busch, Andreas; Day, Taniqua S; Meng, Xing-Li; Yu, Chun I; Dabrowska-Schlepp, Paulina; Fode, Benjamin; Niederkrüger, Holger; Forni, Sabrina; Chen, Shuyuan; Schiffmann, Raphael; Frischmuth, Thomas; Schaaf, Andreas