Ten-Year Follow-Up of Taliglucerase Alfa in Type 1 Gaucher Disease: Real-World Evidence from Albania
阿尔巴尼亚1型戈谢病患者接受Taliglucerase Alfa治疗的十年随访:来自真实世界的证据
期刊:Journal of Clinical Medicine
影响因子:2.9
doi:10.3390/jcm14197015
Cullufi, Paskal; Velmishi, Virtut; Troja, Erjon; Tomori, Sonila; Dervishi, Ermira; Hoxha, Gladiola; Tanka, Marjeta; Pulluqi, Polikron; Perolla, Adela; Basha, Entela; Ivanaj, Arben; Jazexhiu, Eda; Tabaku, Mirela