Morpholino Antisense Oligomers as a Potential Therapeutic Option for the Correction of Alternative Splicing in PMD, SPG2, and HEMS
吗啉代反义寡核苷酸作为PMD、SPG2和HEMS中选择性剪接校正的潜在治疗选择
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2018.05.019
Tantzer, Stephanie; Sperle, Karen; Kenaley, Kaitlin; Taube, Jennifer; Hobson, Grace M
