日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Monitoring biological effects of somatic cell genome editing

监测体细胞基因组编辑的生物学效应

Freedman, Benjamin S; Bulte, Jeff W M; Conklin, Bruce R; Judge, Luke M; Dwinell, Melinda R; Geurts, Aron M; Sitton, Madeleine J; Mahajan, Vineet; Kiani, Samira; Gersbach, Charles A; Ebrahimkhani, Mo R; Kelly, John J; Ronald, John A; Morizane, Ryuji; Gupta, Navin; Shakeri-Zadeh, Ali; Vo, Nicole; Saha, Krishanu; Saxena, Shivani; Gamm, David M; Sinha, Divya; Tarantal, Alice F; Vandsburger, Moriel; Matsubara, Azusa; Fu, Hongxia; Tsai, Shengdar Q

Prenatal Intraportal Delivery of Polymeric Nanoparticles to Fetal Rhesus Monkeys (Macaca mulatta)

向恒河猴胎儿(Macaca mulatta)进行产前门静脉内聚合物纳米颗粒递送

Piotrowski-Daspit, Alexandra S; Lynn, Anna Y; Eaton, David A; Bracaglia, Laura G; Markey, Arianna I; Mortlock, Ryland D; Stitelman, David H; Martinez, Michele L; Lee, Charles C; Kliman, Harvey J; Glazer, Peter M; Tarantal, Alice F; Saltzman, W Mark

The pentameric complex is not required for congenital CMV transmission in seronegative rhesus macaques

五聚体复合物并非血清阴性恒河猴先天性巨细胞病毒传播所必需。

Wang, Hsuan-Yuan; Taher, Husam; Kreklywich, Craig N; Schmidt, Kimberli A; Scheef, Elizabeth A; Barfield, Richard; Otero, Claire E; Valencia, Sarah M; Zhang, Ke; Callahan, Claire; Monticolo, Francesco; Qiao, Yueqing; Gilbride, Roxanne M; Crooks, Chelsea M; Mirza, Anne; Knight, Kelsey; Moström, Matilda J; Manuel, Tabitha D; Sprehe, Lesli; Kendall, Savannah; Burgt, Nathan Vande; Kowalik, Timothy F; Barry, Peter A; Hansen, Scott G; Shu, Jian; Tarantal, Alice F; Chan, Cliburn; Streblow, Daniel N; Picker, Louis J; Kaur, Amitinder; Früh, Klaus; Permar, Sallie R; Malouli, Daniel

Lipid nanoparticle-mediated mRNA delivery to CD34(+) cells in rhesus monkeys.

脂质纳米颗粒介导的mRNA递送至恒河猴CD34(+)细胞

Kim Hyejin, Zenhausern Ryan, Gentry Kara, Lian Liming, Huayamares Sebastian G, Radmand Afsane, Loughrey David, Podilapu Ananda R, Hatit Marine Z C, Ni Huanzhen, Li Andrea, Shajii Aram, Peck Hannah E, Han Keyi, Hua Xuanwen, Jia Shu, Martinez Michele, Lee Charles, Santangelo Philip J, Tarantal Alice, Dahlman James E

Systematic multi-trait AAV capsid engineering for efficient gene delivery

系统性多性状AAV衣壳工程改造以实现高效基因递送

Fatma-Elzahraa Eid ,Albert T Chen ,Ken Y Chan ,Qin Huang ,Qingxia Zheng ,Isabelle G Tobey ,Simon Pacouret ,Pamela P Brauer ,Casey Keyes ,Megan Powell ,Jencilin Johnston ,Binhui Zhao ,Kasper Lage ,Alice F Tarantal ,Yujia A Chan ,Benjamin E Deverman

Engineered IgM and IgG cleaving enzymes for mitigating antibody neutralization and complement activation in AAV gene transfer

工程化IgM和IgG裂解酶用于减轻AAV基因转移中的抗体中和和补体激活

Timothy J Smith ,Zachary C Elmore ,Robert M Fusco ,Joshua A Hull ,Alan Rosales ,Michele Martinez ,Alice F Tarantal ,Aravind Asokan

Correlation of antigen expression with epigenetic modifications after rAAV delivery of a human factor IX variant in mice and rhesus macaques

rAAV递送人凝血因子IX变体后,抗原表达与小鼠和恒河猴表观遗传修饰的相关性

Katja Pekrun ,Calvin J Stephens ,Adriana Gonzalez-Sandoval ,Aranyak Goswami ,Feijie Zhang ,Alice F Tarantal ,Grant Blouse ,Mark A Kay

AAV5 Delivery of CRISPR/Cas9 Mediates Genome Editing in the Lungs of Young Rhesus Monkeys

利用AAV5递送CRISPR/Cas9介导幼年恒河猴肺部基因组编辑

Liang, Shun-Qing; Navia, Andrew W; Ramseier, Michelle; Zhou, Xuntao; Martinez, Michele; Lee, Charles; Zhou, Chen; Wu, Joae; Xie, Jun; Su, Qin; Wang, Dan; Flotte, Terence R; Anderson, Daniel G; Tarantal, Alice F; Shalek, Alex K; Gao, Guangping; Xue, Wen

Expression patterns of CYP26A1, FGF8, CDKN1A, and NPVF in the developing rhesus monkey retina

CYP26A1、FGF8、CDKN1A 和 NPVF 在发育中的恒河猴视网膜中的表达模式

Miranda R Krueger ,Elizabeth Fishman-Williams ,Sergi Simó ,Alice F Tarantal ,Anna La Torre

Rapid molecular imaging of active thrombi in vivo using aptamer-antidote probes

利用适体-解毒剂探针快速对体内活性血栓进行分子成像

Gray, Bethany Powell; Kelly, Linsley; Steen-Burrell, Kady-Ann; Layzer, Juliana M; Rempel, Rachel E; Nimjee, Shahid M; Cooley, Brian C; Tarantal, Alice F; Sullenger, Bruce A