Exploration Into Lived Experiences of Multiple Sulfatase Deficiency-Affected Individuals and Their Families
对多重硫酸酯酶缺乏症患者及其家庭生活经历的探索
期刊:Journal of Child Neurology
影响因子:1.6
doi:10.1177/08830738251339848
Gavazzi, Francesco; Yu, Emily; Tashnim, Zarrin; Woidill, Sarah; Sevagamoorthy, Anjana; Arnold, Kaley; Ammann-Schnell, Louisa; Groeschel, Samuel; Krägeloh-Mann, Ingeborg; Breitling, Vivian; Schlotawa, Lars; Ahrens-Nicklas, Rebecca; Adang, Laura A