Resolution of hepatic fibrosis after ZFN-mediated gene editing in the PiZ mouse model of human α1-antitrypsin deficiency
在PiZ小鼠模型(人类α1-抗胰蛋白酶缺乏症)中,ZFN介导的基因编辑可缓解肝纤维化。
期刊:Hepatology Communications
影响因子:4.6
doi:10.1097/HC9.0000000000000070
Li, Yanfeng; Guha, Chandan; Asp, Patrik; Wang, Xia; Tchaikovskya, Tatyana L; Kim, Kenneth; Mendel, Matthew; Cost, Gregory J; Perlmutter, David H; Roy-Chowdhury, Namita; Fox, Ira J; Conway, Anthony; Roy-Chowdhury, Jayanta