Preferences for potential benefits and risks for gene therapy in the treatment of sickle cell disease
对基因疗法治疗镰状细胞病潜在益处和风险的偏好
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2023009680
Gonzalez Sepulveda, Juan Marcos; Yang, Jui-Chen; Reed, Shelby D; Lee, Ting-Hsuan; Ng, Xinyi; Stothers, Sarah; Irony, Telba; Ho, Martin; Rothman, Jennifer A; Badawy, Sherif; Rowley, Carolyn; Little, Jane; Shah, Nirmish R; Li, Kaiwen; Telen, Marilyn J